Testing effectiveness (Phase 2)Ended earlyNCT03652259
What this trial is testing
Gene Delivery Clinical Trial of SRP-9003 (Bidridistrogene Xeboparvovec) for Participants With Limb-Girdle Muscular Dystrophy, Type 2E (LGMD2E) (Beta-Sarcoglycan Deficiency)
Who this might be right for
Limb-Girdle Muscular Dystrophy, Type 2E
Sarepta Therapeutics, Inc. 6