Not applicableLooking for participantsNCT05653544What this trial is testingNatural History in Primary Mitochondrial MyopathiesWho this might be right forPrimary Mitochondrial Myopathies Cristina Domínguez González 150
Large-scale testing (Phase 3)Study completedNCT05162768What this trial is testingStudy to Evaluate Efficacy and Safety of Elamipretide in Subjects With Primary Mitochondrial Disease From Nuclear DNA Mutations (nPMD)Who this might be right forMitochondrial MyopathiesMitochondrial PathologyMitochondrial DNA Mutation+5 more Stealth BioTherapeutics Inc. 102
Early research (Phase 1)UnknownNCT06186154What this trial is testingVitamin B12 and Folinic Acid Supplementation in Mitochondrial DNA Deletion SyndromesWho this might be right forMitochondrial DNA DeletionMacrocytosis University of British Columbia 25
Early research (Phase 1)WithdrawnNCT04548843What this trial is testingA First in Human Study to Evaluate the Safety of Infusion of MNV-BM-PLC (Autologous CD34+ Cells Enriched With Placenta Derived Allogeneic Mitochondria) in Patients With Primary Mitochondrial Diseases Associated With Mitochondrial DNA Mutation or DeletionWho this might be right forPrimary Mitochondrial Diseases Minovia Therapeutics Ltd.
Not applicableUnknownNCT05029843What this trial is testingSLSMDS Natural History StudyWho this might be right forPearson SyndromeSingle Large Scale Mitochondrial DNA Deletion Syndromes (SLSMDS) The Champ Foundation 30
Not applicableNot Yet RecruitingNCT06907550What this trial is testingMitochondrial DNA Deletions in Plasma as a Diagnostic Aid for Females Presenting With Symptoms of EndometriosisWho this might be right forEndometriosis Pearsanta, Inc 1,000
Not applicableStudy completedNCT05012358What this trial is testingGenomic Profiling of Mitochondrial Disease - Imaging Analysis for Precise Mitochondrial MedicineWho this might be right forMitochondrial MyopathiesMitochondrial DNA MutationMitochondrial Diseases+2 more Mayo Clinic 9
Not applicableEnrolling By InvitationNCT06938542What this trial is testingPalliative Care Needs of Children With Rare Diseases and Their FamiliesWho this might be right forTrisomy 13 SyndromeArthrogryposis Congenita Multiplex With Intestinal AtresiaAsparagine Synthetase Deficiency+16 more Children's National Research Institute 480
Not applicableLooking for participantsNCT01694940What this trial is testingNorth American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)Who this might be right forMitochondrial DisordersMitochondrial Genetic DisordersMitochondrial Diseases+2 more Columbia University 1,000
Not applicableStudy completedNCT03432871What this trial is testingNicotinamide Riboside and Mitochondrial BiogenesisWho this might be right forMitochondrial DiseasesMitochondrial MyopathiesProgressive External Ophthalmoplegia+4 more Cambridge University Hospitals NHS Foundation Trust 13
Not applicableLooking for participantsNCT01793168What this trial is testingRare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at SanfordWho this might be right forRare DisordersUndiagnosed DisordersDisorders of Unknown Prevalence+340 more Sanford Health 20,000