Crick
HomeTrialsGenesDrugs23andMeGraphBlogContact
  • Home
  • Trials
  • Genes
  • Drugs
  • 23andMe
  • Graph
  • Blog
  • Contact
Crick

An open-source clinical intelligence platform. Explore clinical trials, gene networks, and molecular structures using public data sources.

Data Sources

  • ClinicalTrials.gov
  • OpenTargets
  • ClinVar
  • PubChem

Links

  • Contact
  • Privacy

© 2026 Crick. All rights reserved.

Crick is for educational purposes only. Not medical advice.

Results for “Mitochondrial Genetic Disorders”

360 trials

Filters

Phase
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Status
Recruiting
Active, Not Recruiting
Not Yet Recruiting
Completed
Enrolling by Invitation

Showing 20 of 360 results

Testing effectiveness (Phase 2)Study completedNCT01603446
What this trial is testing

L-arginine Therapy on Endothelium-dependent Vasodilation & Mitochondrial Metabolism in MELAS Syndrome

Who this might be right for
MELAS Syndrome
The Hospital for Sick Children 7
Not applicableStudy completedNCT01194141
What this trial is testing

Exercise Training in Barth Syndrome

Who this might be right for
Barth Syndrome
Washington University School of Medicine 4
Not applicableEnded earlyNCT06140329
What this trial is testing

Natural History of Autosomal Dominant Optic Atrophy (ADOA), Caused by OPA1 Mutation

Who this might be right for
Autosomal Dominant Optic AtrophyOptic Atrophy, Autosomal DominantOptic Atrophies, Hereditary+1 more
PYC Therapeutics 1
Testing effectiveness (Phase 2)Not Yet RecruitingNCT07773246
What this trial is testing

Phase 1/2 Study of KRRO-121 in Healthy Volunteers and Patients With UCD

Who this might be right for
Urea Cycle Disorders, InbornUrea Cycle DisordersOrnithine Transcarbamylase (OTC) Deficiency+8 more
Korro Bio, Inc. 30
Post-approval studies (Phase 4)Study completedNCT04801303
What this trial is testing

Evaluation of the Effects of Calcitriol's in the Neurological Symptoms of Friedreich's Ataxia Patients

Who this might be right for
Friedreich Ataxia
Berta Alemany 20
Not applicableStudy completedNCT04649866
What this trial is testing

Coronary Artery Disease in Patients With Friedreich's Ataxia

Who this might be right for
Friedreich Ataxia
University of Pittsburgh 7
Testing effectiveness (Phase 2)Study completedNCT04165239
What this trial is testing

The KHENERGYZE Study

Who this might be right for
Mitochondrial DiseasesMitochondrial MyopathiesMitochondrial Encephalomyopathies+2 more
Khondrion BV 27
Not applicableEnrolling By InvitationNCT06605612
What this trial is testing

Development and Validation of the FBIndex to Determine the Risk of Falls for Patients With Neuromuscular Disorders

Who this might be right for
Inclusion Body MyositisMyotonic DystrophyLimb-girdle and Facioscapulohumeral Muscular Dystrophies+9 more
LMU Klinikum 108
Early research (Phase 1)Study completedNCT04519567
What this trial is testing

Multiple Ascending Dose Study of CTI-1601 Versus Placebo in Subjects With Friedreich's Ataxia

Who this might be right for
Friedreich Ataxia
Larimar Therapeutics, Inc. 27
Not applicableUnknownNCT02114554
What this trial is testing

Mitochondrial nt3243 A>G Mutation in Taiwan

Who this might be right for
MELAS SyndromeNoninsulin-dependent Diabetes Mellitus With Deafness
National Taiwan University Hospital 40
Not applicableStudy completedNCT00002257
What this trial is testing

Controlled Study of the Efficacy and Safety of Maintenance Treatment With Oral Ganciclovir for Newly Diagnosed Cytomegalovirus Retinitis in People With AIDS

Who this might be right for
Cytomegalovirus RetinitisHIV Infections
Hoffmann-La Roche 150
Large-scale testing (Phase 3)Study completedNCT02415127
What this trial is testing

Safety, Tolerability and Efficacy of ACTIMMUNE® Dose Escalation in Friedreich's Ataxia

Who this might be right for
Friedreich's Ataxia
Amgen 92
Testing effectiveness (Phase 2)Looking for participantsNCT06874010
What this trial is testing

A Multiple Ascending Dose Study of DT-216P2 in Patients With Friedreich's Ataxia

Who this might be right for
Friedreich Ataxia
Design Therapeutics, Inc. 20
Large-scale testing (Phase 3)Study completedNCT03293524
What this trial is testing

Efficacy & Safety Study of Bilateral IVT Injection of GS010 in LHON Subjects Due to the ND4 Mutation for up to 1 Year

Who this might be right for
Leber Hereditary Optic Neuropathy
GenSight Biologics 98
Testing effectiveness (Phase 2)Study completedNCT00887562
What this trial is testing

Study of Idebenone in the Treatment of Mitochondrial Encephalopathy Lactic Acidosis & Stroke-like Episodes

Who this might be right for
MELAS Syndrome
Michio Hirano 27
Not applicableStudy completedNCT00000995
What this trial is testing

AZT Plus Ganciclovir in Patients With AIDS and Cytomegalovirus (CMV) Infection

Who this might be right for
Cytomegalovirus InfectionsHIV Infections
National Institute of Allergy and Infectious Diseases (NIAID) 60
Testing effectiveness (Phase 2)Study completedNCT02064569
What this trial is testing

Safety Evaluation of Gene Therapy in Leber Hereditary Optic Neuropathy (LHON) Patients

Who this might be right for
Leber Hereditary Optic Neuropathy
GenSight Biologics 19
Not applicableStudy completedNCT00002222
What this trial is testing

Valganciclovir in the Treatment of Cytomegalovirus (CMV) Retinitis in Patients With AIDS

Who this might be right for
Cytomegalovirus RetinitisHIV Infections
Hoffmann-La Roche 200
Not applicableStudy completedNCT00804102
What this trial is testing

Transcorneal Electrical Stimulation Therapy for Retinal Disease

Who this might be right for
Retinitis PigmentosaMacula OffPrimary Open Angle Glaucoma+8 more
Okuvision GmbH 80
Not applicableLooking for participantsNCT06865482
What this trial is testing

Clinical Course Of Disease In Participants With FA-CM

Who this might be right for
Friedreich AtaxiaCardiomyopathy
Lexeo Therapeutics 65
Next Page