Not applicableStudy completedNCT02638220What this trial is testingCerebrotendinous Xanthomatosis (CTX) Prevalence StudyWho this might be right forCerebrotendinous Xanthomatosis (CTX) Travere Therapeutics, Inc. 442
Early research (Phase 1)Study completedNCT00002854What this trial is testingHigh-Dose Combination Chemotherapy Plus Peripheral Stem Cell Transplantation in Treating Patients With Advanced CancerWho this might be right forCancer City of Hope Medical Center 33
Not applicableUnknownNCT01149005What this trial is testingCystic Fibrosis (CF) Exacerbation and Insulin TreatmentWho this might be right forCystic FibrosisImpaired Glucose TolerancePulmonary Exacerbation Hadassah Medical Organization 30
Post-approval studies (Phase 4)Study completedNCT02170402What this trial is testingChina ADVATE PTP StudyWho this might be right forHemophilia A Baxalta now part of Shire 82
Testing effectiveness (Phase 2)Study completedNCT00283959What this trial is testingA 12-Week Safety and Pharmacodynamic Study of AT1001 (Migalastat Hydrochloride) in Participants With Fabry DiseaseWho this might be right forFabry Disease Amicus Therapeutics 4
Not applicableStudy completedNCT02744066What this trial is testingA Pilot Study to Evaluate Patient Tolerance and Nursing Ease-of-Use of a Novel Hearing Protection DeviceWho this might be right forHearing Impairment Michael Balsan, MD 55
Testing effectiveness (Phase 2)Active Not RecruitingNCT05861453What this trial is testingPharmacokinetics, Pharmacodynamics and Safety of Epeleuton in Patients With Sickle Cell DiseaseWho this might be right forSickle Cell Disease Afimmune 30
Not applicableUnknownNCT01538160What this trial is testingA Single and Low Dose of Recombinant Factor VIIa in Patients With Severe Factor XI Deficiency Undergoing SurgeryWho this might be right forHemophilia C Sheba Medical Center 15
Not applicableStudy completedNCT00001496What this trial is testingEstablishment of Normal Breast Epithelial Cell Lines From Patients at High Risk for Breast CancerWho this might be right forBreast NeoplasmHereditary Neoplastic Syndrome National Cancer Institute (NCI) 50
Not applicableUnknownNCT04388969What this trial is testingWorld Data on Ambroxol for Patients With GD and GBA Related PDWho this might be right forGaucher DiseaseParkinson DiseaseGBA Gene Mutation Shaare Zedek Medical Center 300
Large-scale testing (Phase 3)Study completedNCT00004690What this trial is testingPhase III Study of Monolaurin Cream Therapy for Patients With Congenital IchthyosisWho this might be right forIchthyosis Cellegy Pharmaceuticals 90
Large-scale testing (Phase 3)Study completedNCT01302860What this trial is testingEfficacy, Safety and Tolerability of ACZ885 in Pediatric Patients With the Following Cryopyrin-associated Periodic Syndromes: Familial Cold Autoinflammatory Syndrome, Muckle-Wells Syndrome, or Neonatal Onset Multisystem Inflammatory DiseaseWho this might be right forCryopyrin-associated Periodic SyndromesFamilial Cold Autoinflammatory SyndromeMuckle-Wells Syndrome+1 more Novartis Pharmaceuticals 17
Testing effectiveness (Phase 2)Ended earlyNCT03848182What this trial is testingAnalyzing Childhood Recall Antigens in Patients With Pancreatic CancerWho this might be right forPancreatic Cancer Albert Einstein College of Medicine 10
Not applicableNot Yet RecruitingNCT07095296What this trial is testingEffect of Culturally Tailored Health Education on Postnatal Care Use Among Postpartum Women in EthiopiaWho this might be right forIntervention Swiss Tropical & Public Health Institute 864
Not applicableUnknownNCT03901261What this trial is testingCohort Study of Adult Patients With Down Syndrome at Risk of Developing Alzheimer's Disease (TriAL21)Who this might be right forDown SyndromeAlzheimer Disease Institut Jerome Lejeune 200
Early research (Phase 1)Study completedNCT00101270What this trial is testingOxaliplatin and Irinotecan in Treating Young Patients With Refractory Solid Tumors or LymphomasWho this might be right forChildhood Burkitt LymphomaChildhood Central Nervous System Germ Cell TumorChildhood Diffuse Large Cell Lymphoma+26 more National Cancer Institute (NCI) 24
Not applicableStudy completedNCT01407770What this trial is testingGenetic Susceptibility to Radiation-Induced Skin Reactions in Racial/Ethnic Groups of Patients With Breast CancerWho this might be right forBreast CancerCognitive Ability, GeneralFatigue+4 more Wake Forest University Health Sciences 1,000
Not applicableStudy completedNCT04353466What this trial is testingAssessing the Impact of Elelyso on Bone Involvement Currently Treated With Other ERTsWho this might be right forGaucher Disease, Type 1 Shaare Zedek Medical Center 30
Not applicableNo Longer AvailableNCT03544060What this trial is testingVolanesorsen Early Access Program for Patients With Familial Chylomicronemia Syndrome (FCS)Who this might be right forFamilial Chylomicronemia Akcea Therapeutics
Not applicableUnknownNCT03234582What this trial is testingComparison of RVOT Gradient Under Anaesthesia With Post-operative Gradient in Patients Undergoing TOF RepairWho this might be right forTetralogy of Fallot Post Graduate Institute of Medical Education and Research, Chandigarh 20