Not applicableLooking for participantsNCT03333200What this trial is testingLongitudinal Study of Neurodegenerative DisordersWho this might be right forMLDKrabbe DiseaseALD+24 more University of Pittsburgh 1,500
Large-scale testing (Phase 3)Study completedNCT00004402What this trial is testingPhase III Randomized Study of Interferon Gamma in Children With Severe, Congenital OsteopetrosisWho this might be right forOsteopetrosis FDA Office of Orphan Products Development 30
Not applicableStudy completedNCT02355821What this trial is testingComparative Effects of Moxonidine on Bone Metabolism, Vascular and Cellular Aging in Hypertensive Postmenopausal WomenWho this might be right forOsteopeniaArterial Hypertension National Research Center for Preventive Medicine 114
Testing effectiveness (Phase 2)Active Not RecruitingNCT03301168What this trial is testingStudy of Gene Modified Donor T-cells Following TCR Alpha Beta Positive Depleted Stem Cell TransplantWho this might be right forAcute Lymphoblastic LeukemiaLeukemia, Acute Myeloid (AML), ChildLymphoma, Non-Hodgkin+6 more Bellicum Pharmaceuticals 120
Testing effectiveness (Phase 2)Ended earlyNCT00638820What this trial is testingReduced Intensity AlloTransplant For OsteopetrosisWho this might be right forOsteopetrosis Masonic Cancer Center, University of Minnesota 3
Not applicableLooking for participantsNCT04528355What this trial is testingData Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RICWho this might be right forPrimary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+2 more Paul Szabolcs 50
Not applicableStudy completedNCT07133256What this trial is testingEffects of Aerobic Versus Resistance Training on Bone Metabolism in Stage 3-4 Chronic Kidney DiseaseWho this might be right forOsteopeniaBone Metabolism DisordersChronic Kidney Disease (Stage 3-4)+1 more Sinai University 60
Large-scale testing (Phase 3)Study completedNCT01019876What this trial is testingRisk-Adapted Allogeneic Stem Cell Transplantation For Mixed Donor Chimerism In Patients With Non-Malignant DiseasesWho this might be right forBone Marrow FailureOsteopetrosisFanconi Anemia+1 more Columbia University 38
Testing effectiveness (Phase 2)Study completedNCT02584608What this trial is testingUse of ACTIMMUNE in Patients With ADO2Who this might be right forAutosomal Dominant Osteopetrosis Type 2 Indiana University 12
Not applicableStudy completedNCT00043329What this trial is testingPost Marketing Surveillance Study of Actimmune in Patients With Severe, Malignant OsteopetrosisWho this might be right forOsteopetrosis InterMune 6
Testing effectiveness (Phase 2)Looking for participantsNCT01962415What this trial is testingReduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCTWho this might be right forPrimary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+4 more Paul Szabolcs 100
Not applicableNo Longer AvailableNCT01200017What this trial is testingExpanded Access Protocol (EAP) Using the CliniMACS® Device for Pediatric Haplocompatible Donor Stem Cell TransplantWho this might be right forAcute Lymphoblastic LeukemiaAcute Myeloid LeukemiaChronic Myeloid Leukemia+9 more Christopher Dvorak
Large-scale testing (Phase 3)UnknownNCT01087398What this trial is testingHematopoietic Stem Cell Transplantation for Malignant Infantile OsteopetrosisWho this might be right forOsteopetrosis Tehran University of Medical Sciences 10
Very early researchUnknownNCT03691311What this trial is testingBiomarker Study of the Antitumoral Activity of Denosumab in the Pre- Operative Setting of Early Breast CancerWho this might be right forBreast Neoplasm FemaleStage I Breast CancerStage II Breast Cancer+2 more Institut Català d'Oncologia 60
Not applicableStudy completedNCT06521580What this trial is testingOutcomes of Patients With Osteopetrosis Weight-bearing Bone FracturesWho this might be right forOsteopetrosis Kasr El Aini Hospital 6
Testing effectiveness (Phase 2)Ended earlyNCT02065869What this trial is testingSafety Study of Gene Modified Donor T-cells Following TCRαβ+ Depleted Stem Cell TransplantWho this might be right forAcute Lymphoblastic LeukemiaLeukemia, Acute Myeloid (AML), ChildLymphoma, Non-Hodgkin+10 more Bellicum Pharmaceuticals 187
Testing effectiveness (Phase 2)Study completedNCT00730314What this trial is testingUnrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood CellsWho this might be right forSickle Cell DiseaseThalassemiaAnemia+9 more Children's Hospital Los Angeles 25
Testing effectiveness (Phase 2)Study completedNCT02666768What this trial is testingACTIMMUNE in Intermediate OsteopetrosisWho this might be right forOsteopetrosis Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center 5
Not applicableStudy completedNCT07102810What this trial is testingHypnosis-Based Machine Learning Biomarker StudyWho this might be right forDisorder; TranceAnxiety Icahn School of Medicine at Mount Sinai 50
Early research (Phase 1)Ended earlyNCT00145886What this trial is testingRhPTH Therapy for Low Turnover Bone FragilityWho this might be right forOsteopetrosis University of Chicago 2