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Results for “Paroxysmal Nocturnal Haemoglobinuria”

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Showing 20 of 0 results

Not applicableActive Not RecruitingNCT03329365
What this trial is testing

Paroxysmal Nocturnal Hemoglobinuria in ESUS & ETUS

Who this might be right for
Paroxysmal Nocturnal HemoglobinuriaEmbolic Stroke of Undetermined SourceTransient Ischemic Attack+1 more
London Health Sciences Centre Research Institute OR Lawson Research Institute of St. Joseph's 200
Not applicableUnknownNCT01224483
What this trial is testing

Multicenter Retrospective Analysis About the Clinical Characteristics of Korean Paroxysmal Nocturnal Hemoglobinuria (PNH) Patients

Who this might be right for
Hemoglobinuria, Paroxysmal
Samsung Medical Center 350
Early research (Phase 1)Study completedNCT05490017
What this trial is testing

To Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Escalating Single and Multiple Doses of KP104

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Kira Pharmacenticals (US), LLC. 80
Post-approval studies (Phase 4)Study completedNCT04320602
What this trial is testing

Ravulizumab in Adult Participants With Paroxysmal Nocturnal Hemoglobinuria Currently Treated With High-Dose Eculizumab

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Alexion Pharmaceuticals, Inc. 18
Not applicableStudy completedNCT01364363
What this trial is testing

Unrelated Donor Stem Cell Transplantation

Who this might be right for
Severe Aplastic AnemiaParoxysmal Nocturnal HemoglobinuriaAcute Myelogenous Leukemia+10 more
Scripps Health 64
Early research (Phase 1)Looking for participantsNCT07760467
What this trial is testing

To Evaluate Safety, Tolerability, PK/PD & Food Effect of Single/Multiple Oral TUL321 Capsules in Healthy Participants.

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria, PNH
Zhuhai United Laboratories Co., Ltd. 94
Large-scale testing (Phase 3)Study completedNCT03406507
What this trial is testing

Ravulizumab (ALXN1210) in Children and Adolescents With Paroxysmal Nocturnal Hemoglobinuria

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Alexion Pharmaceuticals, Inc. 13
Testing effectiveness (Phase 2)Not Yet RecruitingNCT07266155
What this trial is testing

Efficacy, Safety, and Pharmacokinetics of LP-005 Injection in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Longbio Pharma 30
Not applicableStudy completedNCT00856388
What this trial is testing

Fludarabine Phosphate, Melphalan, Total-Body Irradiation, Donor Stem Cell Transplant in Treating Patients With Hematologic Cancer or Bone Marrow Failure Disorders

Who this might be right for
Accelerated Phase Chronic Myelogenous LeukemiaAcute Myeloid Leukemia With Multilineage Dysplasia Following Myelodysplastic SyndromeAdult Acute Lymphoblastic Leukemia in Remission+97 more
Roswell Park Cancer Institute 62
Not applicableEnded earlyNCT07036718
What this trial is testing

NIS PDC the Efficacy and Safety of Iptacopan in Adults in Routine Clinical Practice

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Novartis Pharmaceuticals 6
Testing effectiveness (Phase 2)Active Not RecruitingNCT06764303
What this trial is testing

NTQ5082 Capsules in the Treatment of Paroxysmal Nocturnal Hemoglobinuria Patients

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Nanjing Chia-tai Tianqing Pharmaceutical 24
Testing effectiveness (Phase 2)Study completedNCT03439839
What this trial is testing

Study of Safety, Efficacy, Tolerability, Pharmacokinetics and Pharmacodynamics of LNP023 in in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria (PNH) With Signs of Active Hemolysis
Novartis Pharmaceuticals 16
Not applicableStudy completedNCT04671810
What this trial is testing

Prospective Observational Study of Long-term Pathogenic Treatment of Elizaria®

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
AO GENERIUM 44
Early research (Phase 1)Study completedNCT02264639
What this trial is testing

A Phase I Study to Assess the Safety of Pegcetacoplan (APL-2) as an Add-On to Standard of Care in Subjects With PNH

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Apellis Pharmaceuticals, Inc. 9
Large-scale testing (Phase 3)Active Not RecruitingNCT04654468
What this trial is testing

A Study Evaluating the Efficacy, Safety, Pharmacokinetics and Pharmacodynamics of Crovalimab in Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH) Not Previously Treated With Complement Inhibition

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Hoffmann-La Roche 51
Testing effectiveness (Phase 2)Study completedNCT03946748
What this trial is testing

Study to Evaluate the Efficacy and Safety of REGN3918 in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Regeneron Pharmaceuticals 24
Not applicableActive Not RecruitingNCT05776472
What this trial is testing

A Real World Effectiveness Study of Pegcetacoplan in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Swedish Orphan Biovitrum 165
Large-scale testing (Phase 3)Study completedNCT04060264
What this trial is testing

Clinical Trial of BCD-148 and Soliris® for the Treatment of Patients With Paroxysmal Nocturnal Hemoglobinuria

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria
Biocad 28
Testing effectiveness (Phase 2)Study completedNCT02352493
What this trial is testing

An Investigational Drug, ALN-CC5, in Healthy Adult Volunteers and Patients With PNH

Who this might be right for
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Alnylam Pharmaceuticals 62
Not applicableAvailableNCT05222412
What this trial is testing

Managed Access Programs for LNP023, Iptacopan

Who this might be right for
C3 Glomerulopathy (C3G)Paroxysmal Nocturnal Hemoglobinuria (PNH)
Novartis Pharmaceuticals
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