Large-scale testing (Phase 3)Ended earlyNCT04925960
What this trial is testing
Oral Epalrestat Therapy in Pediatric Subjects With PMM2-CDG
Who this might be right for
Pmm2-CDGPhosphomannomutase 2 DeficiencyPhosphomannomutase 2 Congenital Disorder of Glycosylation+2 more
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