Not applicableActive Not RecruitingNCT03173300What this trial is testingNatural History Study Protocol in PMM2-CDG (CDG-Ia)Who this might be right forPhosphomannomutase 2 Deficiency Glycomine, Inc. 120
Large-scale testing (Phase 3)Active Not RecruitingNCT06892288What this trial is testingAssess the Efficacy and Safety of Weekly Doses of GLM101 in Participants With PMM2-CDGWho this might be right forPhosphomannomutase 2 DeficiencyPMM2-CDG Glycomine, Inc. 50
Large-scale testing (Phase 3)Ended earlyNCT04925960What this trial is testingOral Epalrestat Therapy in Pediatric Subjects With PMM2-CDGWho this might be right forPmm2-CDGPhosphomannomutase 2 DeficiencyPhosphomannomutase 2 Congenital Disorder of Glycosylation+2 more Maggie's Pearl, LLC 42
Testing effectiveness (Phase 2)Enrolling By InvitationNCT06657859What this trial is testingOpen-Label Extension Study to Assess GLM101 in PMM2-CDG PatientsWho this might be right forPmm2-CDGPhosphomannomutase 2 Deficiency Glycomine, Inc. 40
Testing effectiveness (Phase 2)Study completedNCT05549219What this trial is testing24-Week Study to Assess the PD, Safety, Tolerability, and PK of GLM101 in Participants With PMM2-CDGWho this might be right forPmm2-CDGPhosphomannomutase 2 Deficiency Glycomine, Inc. 27
Not applicableLooking for participantsNCT04199000What this trial is testingClinical and Basic Investigations Into Congenital Disorders of GlycosylationWho this might be right forCongenital Disorders of Glycosylation Icahn School of Medicine at Mount Sinai 500
Large-scale testing (Phase 3)Ended earlyNCT04679389What this trial is testingAcetazolamide Efficacy in Ataxia in PMM2-CDGWho this might be right forPmm2-CDGCDG1A Mayo Clinic 25