Not applicableStudy completedNCT03067142What this trial is testingProteomics of Primary Hyperoxaluria Type 1Who this might be right forPrimary Hyperoxaluria Type 1 Ann & Robert H Lurie Children's Hospital of Chicago 93
Not applicableLooking for participantsNCT06225882What this trial is testingRetrospective and Prospective Follow-up of Patients With Primary Hyperoxaluria Type 1 Treated With Lumasiran in France.Who this might be right forPatients With PH1 Treated With Lumasiran in France Hospices Civils de Lyon 100
Not applicableApproved For MarketingNCT04125472What this trial is testingExpanded Access Protocol to Provide Lumasiran to Patients With Primary Hyperoxaluria Type 1Who this might be right forPrimary Hyperoxaluria Alnylam Pharmaceuticals
Testing effectiveness (Phase 2)Study completedNCT03847909What this trial is testingEvaluate DCR-PHXC in Children and Adults With Primary Hyperoxaluria Type 1 and Primary Hyperoxaluria Type 2Who this might be right forPrimary Hyperoxaluria Type 1 (PH1)Primary Hyperoxaluria Type 2 (PH2)Kidney Diseases+2 more Novo Nordisk A/S 35
Not applicableLooking for participantsNCT00588562What this trial is testingRare Kidney Stone Consortium Patient RegistryWho this might be right forPrimary HyperoxaluriaDent DiseaseCystinuria+1 more Mayo Clinic 730
Not applicableStudy completedNCT02830009What this trial is testingIDENTIFICATION OF A MULTI-ANALYTE PROFILE FOR PRIMARY HYPEROXALURIA AND COMPARISON WITH HEALTHY SIBLINGS AND IDIOPATHIC HYPERCALCIURIAWho this might be right forPrimary Hyperoxaluria Type 1Idiopathic Hypercalciuria Hospices Civils de Lyon 5
Large-scale testing (Phase 3)Study completedNCT03681184What this trial is testingEvaluate Lumasiran in Children and Adults With Primary Hyperoxaluria Type 1Who this might be right forPrimary Hyperoxaluria Type 1 (PH1) Alnylam Pharmaceuticals 39
Not applicableActive Not RecruitingNCT04982393What this trial is testingBONAPH1DE, A Prospective Observational Study of Patients With Primary Hyperoxaluria Type 1 (PH1)Who this might be right forPrimary Hyperoxaluria Type 1 Alnylam Pharmaceuticals 207
Not applicableLooking for participantsNCT02026388What this trial is testingRare Kidney Stone Consortium BiobankWho this might be right forPrimary HyperoxaluriaDent DiseaseAPRT Deficiency+1 more Mayo Clinic 2,000
Early research (Phase 1)Ended earlyNCT02795325What this trial is testingDCR-PH1 in Patients With Primary Hyperoxaluria Type 1 (PH1)Who this might be right forPrimary Hyperoxaluria Type 1 Dicerna Pharmaceuticals, Inc., a Novo Nordisk company 41
Not applicableEnrolling By InvitationNCT03655223What this trial is testingEarly Check: Expanded Screening in NewbornsWho this might be right forSpinal Muscular AtrophyFragile X SyndromeFragile X - Premutation+182 more RTI International 30,000
Not applicableNo Longer AvailableNCT05993416What this trial is testingTreatment of Primary Hyperoxaluria Type 1 With NedosiranWho this might be right forPrimary Hyperoxaluria Type 1 (PH1) Dicerna Pharmaceuticals, Inc., a Novo Nordisk company
Testing effectiveness (Phase 2)Study completedNCT02706886What this trial is testingStudy of Lumasiran in Healthy Adults and Patients With Primary Hyperoxaluria Type 1Who this might be right forPrimary Hyperoxaluria Type 1 (PH1) Alnylam Pharmaceuticals 52
Testing effectiveness (Phase 2)Looking for participantsNCT04580420What this trial is testingSafety & Efficacy of DCR-PHXC in Patients With PH1 and ESRDWho this might be right forPrimary Hyperoxaluria Type 1End Stage Renal Disease Dicerna Pharmaceuticals, Inc., a Novo Nordisk company 28
Large-scale testing (Phase 3)Study completedNCT03905694What this trial is testingLumasiran in Infants and Young Children With Primary Hyperoxaluria Type 1Who this might be right forPrimary HyperoxaluriaPrimary Hyperoxaluria Type 1 (PH1) Alnylam Pharmaceuticals 18
Testing effectiveness (Phase 2)Study completedNCT03350451What this trial is testingAn Extension Study of an Investigational Drug, Lumasiran (ALN-GO1), in Participants With Primary Hyperoxaluria Type 1Who this might be right forPH1Primary HyperoxaluriaRNAi Therapeutic+2 more Alnylam Pharmaceuticals 20
Not applicableLooking for participantsNCT06283082What this trial is testingOxalate Excretion Profile in Patients with a Heterozygous Mutation of the AGXT (alanine-glyoxylate Aminotransferase) GeneWho this might be right forHyperoxaluria (Disorder) Hospices Civils de Lyon 25
Large-scale testing (Phase 3)Active Not RecruitingNCT04042402What this trial is testingLong Term Extension Study in Patients With Primary HyperoxaluriaWho this might be right forPrimary Hyperoxaluria Type 1 (PH1)Primary Hyperoxaluria Type 2 (PH2)Kidney Diseases+3 more Dicerna Pharmaceuticals, Inc., a Novo Nordisk company 75
Testing effectiveness (Phase 2)Looking for participantsNCT06839235What this trial is testingPhase 1/2 Study of ABO-101 in Primary Hyperoxaluria Type 1 (redePHine)Who this might be right forPrimary Hyperoxaluria Type 1 (PH1) Arbor Biotechnologies 23
Very early researchActive Not RecruitingNCT06892301What this trial is testingClinical Exploration Study of YOLT-203 in the Treatment of Type 1 Primary Hyperoxaluria (PH1)Who this might be right forType 1 Primary Hyperoxaluria Guangzhou Women and Children's Medical Center 2