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Results for “RARE DISEASE”

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Showing 20 of 0 results

Not applicableLooking for participantsNCT06193850
What this trial is testing

Protocol N. 2014 - Observational Study on the Quality of Life of Outpatients

Who this might be right for
Urologic DiseasesMale InfertilitySexual Medicine
IRCCS San Raffaele 10,000
Testing effectiveness (Phase 2)Ended earlyNCT02702115
What this trial is testing

Ascending Dose Study of Genome Editing by the Zinc Finger Nuclease (ZFN) Therapeutic SB-318 in Subjects With MPS I

Who this might be right for
MPS I
Sangamo Therapeutics 3
Testing effectiveness (Phase 2)Looking for participantsNCT01356290
What this trial is testing

Antiangiogenic Therapy for Children With Recurrent Medulloblastoma, Ependymoma, ATRT and Rare CNS Tumors

Who this might be right for
Medulloblastoma RecurrentEpendymoma RecurrentATRT Recurrent+1 more
Medical University of Vienna 232
Large-scale testing (Phase 3)UnknownNCT00004487
What this trial is testing

Phase III Study of Chondrocyte Alginate Gel Suspension in Pediatric Patients With Vesicoureteral Reflux

Who this might be right for
Vesicoureteral Reflux
FDA Office of Orphan Products Development 60
Not applicableEnded earlyNCT03955276
What this trial is testing

An Open Label Navigational Investigation of Molecular Profile-Related Evidence Determining Individualized Cancer Therapy for Patients With Incurable Hematologic Malignancies (I-PREDICT Heme)

Who this might be right for
Hematologic Cancer
University of California, San Diego 13
Not applicableWithdrawnNCT06560346
What this trial is testing

Understanding the Natural History Early in the Course or Presentation of Friedreich Ataxia

Who this might be right for
Friedreich AtaxiaRare Diseases
Friedreich's Ataxia Research Alliance
Not applicableStudy completedNCT00006134
What this trial is testing

Study of the Predictors of the Course and Early Outcome of Patients With Systemic Lupus Erythematosus: Nature Versus Nurture

Who this might be right for
Systemic Lupus Erythematosus
National Center for Research Resources (NCRR) 300
Early research (Phase 1)Looking for participantsNCT02897063
What this trial is testing

Effects of Midodrine and Droxidopa on Splanchnic Capacitance in Autonomic Failure

Who this might be right for
Autonomic FailurePure Autonomic FailureMultiple System Atrophy+2 more
Vanderbilt University Medical Center 34
Not applicableStudy completedNCT00960609
What this trial is testing

Communicating Veins Between Adjacent Hepatic Veins: an Intra-operative Ultrasound Study

Who this might be right for
Liver Tumors
University of Milan
Testing effectiveness (Phase 2)Study completedNCT00004464
What this trial is testing

Study of High Dose Cyclophosphamide in Patients With Severe Aplastic Anemia and Paroxysmal Nocturnal Hemoglobinuria

Who this might be right for
Aplastic AnemiaParoxysmal Hemoglobinuria, Nocturnal
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins 69
Not applicableNot Yet RecruitingNCT07130071
What this trial is testing

Channelling Algorithm Proficiency To Understand, Recognise and Elucidate Disease

Who this might be right for
Rare Disorders
Research in Real-Life Ltd 500
Not applicableNot Yet RecruitingNCT07650799
What this trial is testing

AI-assisted Rare Disease Diagnosis

Who this might be right for
Rare DisordersRare Diseases
Peking Union Medical College Hospital 1,056
Not applicableStudy completedNCT06109012
What this trial is testing

Multiple Disseminated Hydatidosis With Rare Locations

Who this might be right for
Echinococcus Infections
Faculty Of Medicine And Pharmacy, Casablanca 1
Large-scale testing (Phase 3)Study completedNCT00659100
What this trial is testing

A Trial to Assess Consumer Self-Selection and Use of Gabapentin for Occasional Sleeplessness in an Over-the-Counter Environment

Who this might be right for
Transient Insomnia
Pfizer's Upjohn has merged with Mylan to form Viatris Inc. 1,254
Testing effectiveness (Phase 2)Study completedNCT00141765
What this trial is testing

Study of High-Dose Chemotherapy With Bone Marrow or Stem Cell Transplant for Rare Poor-Prognosis Cancers

Who this might be right for
Wilms TumorFibrosarcomaCarcinoma, Round Cell+2 more
University of Michigan Rogel Cancer Center 25
Post-approval studies (Phase 4)Study completedNCT01250951
What this trial is testing

This Study Will Evaluate Efficacy and Safety of Deferasirox in Patients With Myelodysplastic Syndromes (MDS), Thalassemia and Rare Anemia Types Having Transfusion-induced Iron Overload.

Who this might be right for
Myelodysplastic SyndromeThalassemia
Novartis Pharmaceuticals 111
Testing effectiveness (Phase 2)Ended earlyNCT00004466
What this trial is testing

Pilot Study of Atorvastatin in Children With Chronic Hyperlipidemia Secondary to Nephrotic Syndrome

Who this might be right for
Nephrotic SyndromeHyperlipidemia
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) 5
Testing effectiveness (Phase 2)Study completedNCT00004275
What this trial is testing

Oxandrolone Compared With a Placebo on Growth Rate in Girls With Growth Hormone-Treated Turner's Syndrome

Who this might be right for
Turner's Syndrome
National Institute of Neurological Disorders and Stroke (NINDS) 80
Not applicableStudy completedNCT00646828
What this trial is testing

Cardiovascular Evaluation of Adult PHA 1 Patients

Who this might be right for
Pseudohypoaldosteronism Type 1
Assistance Publique - Hôpitaux de Paris 98
Not applicableWithdrawnNCT02724995
What this trial is testing

Finding Genes for Rare Diseases

Who this might be right for
Rare Diseases
University of Kentucky
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