Very early researchLooking for participantsNCT07066085What this trial is testingSerial Blood Count StudyWho this might be right forCyclic NeutropeniaCongenital NeutropeniaNeutropenia University of Washington 20
Testing effectiveness (Phase 2)Enrolling By InvitationNCT01852370What this trial is testingSequential Cadaveric Lung and Bone Marrow Transplant for Immune Deficiency DiseasesWho this might be right forSevere Combined Immunodeficiency (SCID)Immunodeficiency With Predominant T-cell Defect, UnspecifiedSevere Chronic Neutropenia+6 more Paul Szabolcs 16
Testing effectiveness (Phase 2)Not Yet RecruitingNCT04844177What this trial is testingTotal Lymphoid Irradiation Pre-HSCT in Severe Congenital NeutropeniaWho this might be right forSevere Congenital NeutropeniaGATA2 Deficiency Federal Research Institute of Pediatric Hematology, Oncology and Immunology 10
Large-scale testing (Phase 3)Study completedNCT00008359What this trial is testingCaspofungin Acetate Compared With Amphotericin B Liposomal in Treating Patients With Persistent Fever and Neutropenia Following Cancer TreatmentWho this might be right forCancer Memorial Sloan Kettering Cancer Center
Early research (Phase 1)Study completedNCT05078879What this trial is testingEmpagliflozin as a Treatment for Severe Congenital Neutropenia Due to G6PC3 DeficiencyWho this might be right forCrohn's DiseaseGlycogen MetabolismInflammatory Bowel Disease (IBD) National Institute of Allergy and Infectious Diseases (NIAID) 4
Large-scale testing (Phase 3)Study completedNCT00003938What this trial is testingLiposomal Amphotericin B in Treating Granulocytopenia and Persistent Unexplained Fever in Cancer PatientsWho this might be right forCancer European Organisation for Research and Treatment of Cancer - EORTC 115
Testing effectiveness (Phase 2)Active Not RecruitingNCT02061800What this trial is testingCD34+ (Malignant) Stem Cell Selection for Patients Receiving Allogenic Stem Cell TransplantWho this might be right forChronic Myeloid Leukemia (CML)Acute Myelogenous Leukemia (AML)Myelodysplastic Syndrome (MDS)+3 more Diane George 14
Large-scale testing (Phase 3)Looking for participantsNCT06056297What this trial is testingMavorixafor in Participants With Congenital and Acquired Primary Autoimmune and Idiopathic Chronic Neutropenic Disorders Who Are Experiencing Recurrent and/or Serious InfectionsWho this might be right forNeutropenia X4 Pharmaceuticals 176
Not applicableEnded earlyNCT02179359What this trial is testingHematopoietic Stem Cell Transplant for High Risk HemoglobinopathiesWho this might be right forSickle Cell DiseaseTransfusion Dependent Alpha- or Beta- ThalassemiaDiamond Blackfan Anemia+5 more Masonic Cancer Center, University of Minnesota 38
Not applicableStudy completedNCT05687474What this trial is testingBaby Detect : Genomic Newborn ScreeningWho this might be right forCongenital Adrenal HyperplasiaFamilial Hyperinsulinemic Hypoglycemia 1Phosphoglucomutase 1 Deficiency+121 more Centre Hospitalier Universitaire de Liege 6,824
Not applicableEnded earlyNCT00062231What this trial is testingMoxifloxacin Compared With Ciprofloxacin/Amoxicillin in Treating Fever and Neutropenia in Patients With CancerWho this might be right forChronic Myeloproliferative DisordersFever, Sweats, and Hot FlashesInfection+8 more European Organisation for Research and Treatment of Cancer - EORTC 351
Large-scale testing (Phase 3)Study completedNCT00176852What this trial is testingStem Cell Transplant for HemoglobinopathyWho this might be right forSickle Cell DiseaseThalassemiaSevere Congenital Neutropenia+2 more Masonic Cancer Center, University of Minnesota 22
Early research (Phase 1)Study completedNCT01917708What this trial is testingBone Marrow Transplant With Abatacept for Non-Malignant DiseasesWho this might be right forHurler SyndromeFanconi AnemiaGlanzmann Thrombasthenia+12 more Emory University 10
Not applicableStudy completedNCT02866162What this trial is testingScreening for Genes in Patients With Congenital NeutropeniaWho this might be right forCongenital Neutropenia Centre Hospitalier Universitaire Dijon 25
Testing effectiveness (Phase 2)Study completedNCT00730314What this trial is testingUnrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood CellsWho this might be right forSickle Cell DiseaseThalassemiaAnemia+9 more Children's Hospital Los Angeles 25
Testing effectiveness (Phase 2)Study completedNCT00305708What this trial is testingBusulfan, Antithymocyte Globulin, and Fludarabine Followed By a Donor Stem Cell Transplant in Treating Young Patients With Blood Disorders, Bone Marrow Disorders, Chronic Myelogenous Leukemia in First Chronic Phase, or Acute Myeloid Leukemia in First RemissionWho this might be right forCongenital Amegakaryocytic ThrombocytopeniaDiamond-blackfan AnemiaFanconi Anemia+3 more University of California, San Francisco 40
Testing effectiveness (Phase 2)Study completedNCT03513328What this trial is testingConditioning Regimen for Allogeneic Hematopoietic Stem-Cell TransplantationWho this might be right forBone Marrow Failure SyndromeThalassemiaSickle Cell Disease+13 more University of Florida 6
Not applicableLooking for participantsNCT06999954What this trial is testingShwachman-Diamond Syndrome Global Patient Survey and Partnering PlatformWho this might be right forShwachman-Diamond SyndromeSDSIBMF+24 more Shwachman-Diamond Syndrome Alliance Inc 8,000
Not applicableLooking for participantsNCT02720679What this trial is testingInvestigation of the Genetics of Hematologic DiseasesWho this might be right forBone Marrow Failure SyndromesErythrocyte DisorderLeukocyte Disorder+10 more St. Jude Children's Research Hospital 1,716
Not applicableStudy completedNCT00244010What this trial is testingPartially Matched Stem Cell Transplantation for Patients With Refractory Severe Aplastic Anemia or Refractory CytopeniasWho this might be right forAnemia, AplasticAmegakaryocytic ThrombocytopeniaDiamond-Blackfan Anemia+1 more St. Jude Children's Research Hospital 4