Crick
HomeTrialsGenesDrugs23andMeGraphBlogContact
  • Home
  • Trials
  • Genes
  • Drugs
  • 23andMe
  • Graph
  • Blog
  • Contact
Crick

An open-source clinical intelligence platform. Explore clinical trials, gene networks, and molecular structures using public data sources.

Data Sources

  • ClinicalTrials.gov
  • OpenTargets
  • ClinVar
  • PubChem

Links

  • Contact
  • Privacy

© 2026 Crick. All rights reserved.

Crick is for educational purposes only. Not medical advice.

Results for “Severe Thalassemia”

Filters

Phase
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Status
Recruiting
Active, Not Recruiting
Not Yet Recruiting
Completed
Enrolling by Invitation

Showing 20 of 0 results

Large-scale testing (Phase 3)Looking for participantsNCT05477563
What this trial is testing

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

Who this might be right for
Beta-ThalassemiaThalassemiaHematologic Diseases+4 more
Vertex Pharmaceuticals Incorporated 26
Not applicableStudy completedNCT04526405
What this trial is testing

Frequency of COVID-19 Antibodies in Patients With Hereditary Hematological Diseases

Who this might be right for
Thalassemia MajorCovid19
University of Milano Bicocca 63
Post-approval studies (Phase 4)Study completedNCT00171301
What this trial is testing

Extension Study of the Efficacy and Safety of Deferasirox Treatment in Beta-thalassemia Patients With Transfusional Hemosiderosis (Study Amended to 2-year Duration)

Who this might be right for
Beta-thalassemia MajorHemosiderosisIron Overload+1 more
Novartis Pharmaceuticals 233
Not applicableActive Not RecruitingNCT06875219
What this trial is testing

To Evaluate Long- Term Safety and Efficacy of Luspatercept

Who this might be right for
Thalassemia Major
Fondazione per la Ricerca sulle Anemie ed Emoglobinopatie in Italia 350
Not applicableEnded earlyNCT02179359
What this trial is testing

Hematopoietic Stem Cell Transplant for High Risk Hemoglobinopathies

Who this might be right for
Sickle Cell DiseaseTransfusion Dependent Alpha- or Beta- ThalassemiaDiamond Blackfan Anemia+5 more
Masonic Cancer Center, University of Minnesota 38
Post-approval studies (Phase 4)UnknownNCT00887081
What this trial is testing

Interferon and Ribavirin Treatment in Patients With Hemoglobinopathies

Who this might be right for
Hemoglobinopathies
Azienda Ospedaliera V. Cervello 150
Not applicableUnknownNCT02067130
What this trial is testing

Utility of Fibroscan in Estimating Hepatic Iron Concentration

Who this might be right for
Hereditary Anemias
University of British Columbia 30
Not applicableStudy completedNCT01206075
What this trial is testing

Evaluating the Safety and Effectiveness of Mozobil Mobilization in Adults With Beta-Thalassemia Major

Who this might be right for
Beta-Thalassemia
University of Washington 20
Not applicableUnknownNCT06137079
What this trial is testing

"Iron Overload and Endocrinological Diseases"

Who this might be right for
Iron OverloadThalassemia MajorThalassemia Intermedia+2 more
Azienda Ospedaliero-Universitaria di Modena 62
Testing effectiveness (Phase 2)Study completedNCT01709032
What this trial is testing

Combination Deferasirox and Deferiprone for Severe Iron Overload in Thalassemia

Who this might be right for
Thalassemia Major With Severe Transfusional Iron Overload
Children's Hospital of Philadelphia 9
Large-scale testing (Phase 3)UnknownNCT02173951
What this trial is testing

An Algorithm to Start Iron Chelation in Minimally Transfused Young Beta-thalassemia Major Patients

Who this might be right for
Beta Thalassemia Major
Ain Shams University 64
Post-approval studies (Phase 4)Study completedNCT02342145
What this trial is testing

Efficacy of Basiliximab in the Prevention of Acute Graft-versus-host Disease in Unrelated Allogeneic Hematopoietic Stem Cell Transplantation Therapy for Thalassemia Major

Who this might be right for
Beta-Thalassemia MajorGraft-versus-host Disease (GVHD)
Zhongming Zhang 205
Testing effectiveness (Phase 2)Study completedNCT00390858
What this trial is testing

A 4-year Extension Study to Core 1-year Study of Iron Chelation Therapy With Deferasirox in β-thalassemia Major Pediatric Patients With Transfusional Iron Overload.

Who this might be right for
Transfusional Iron Overloadβ-thalassemia MajorPediatric Rare Anemia
Novartis Pharmaceuticals 40
Early research (Phase 1)Ended earlyNCT02231710
What this trial is testing

Safety Study of Gene Modified Donor T Cell Infusion After Stem Cell Transplant for Non-Malignant Diseases

Who this might be right for
Primary Immune Deficiency DisordersHemophagocytic LymphohistiocytosisInherited Bone Marrow Failure Syndrome+2 more
Bellicum Pharmaceuticals 1
Post-approval studies (Phase 4)UnknownNCT02984475
What this trial is testing

The Potential Hepatoprotective Effect of Metformin in Patients With Beta Thalassemia Major

Who this might be right for
Beta Thalassemia Major Anemia
Cairo University 60
Testing effectiveness (Phase 2)Looking for participantsNCT05693909
What this trial is testing

A Trial Testing SP-420 in Subjects With Transfusion-dependent β-thalassemia or Low-risk Myelodysplastic Syndromes

Who this might be right for
Beta Thalassemia Major AnemiaMyelodysplastic Syndrome
Pharmacosmos A/S 90
Not applicableStudy completedNCT06831799
What this trial is testing

ERN-EuroBloodNet Registry on Patients With Rare Red Blood Cell Defects and COVID-19

Who this might be right for
HemoglobinopathiesSickle Cell DiseaseSickle Cell Anemia+21 more
Hospital Universitari Vall d'Hebron Research Institute 684
Post-approval studies (Phase 4)WithdrawnNCT01724138
What this trial is testing

An Open Label Study to Evaluate the Pharmacokinetics, Safety, Tolerability and Efficacy of Deferasirox Administered to Chinese Patients With β-thalassemia Major Aged From 2 to Less Than 6 Years Old

Who this might be right for
β-thalassemia Major
Novartis Pharmaceuticals
Not applicableStudy completedNCT04367701
What this trial is testing

Congenital Heart Surgery in Pediatric Patients With Beta-Thalassemia Major

Who this might be right for
Hemolysis
Ain Shams University 41
Not applicableUnknownNCT03951818
What this trial is testing

Observing the Changes of Endocrine and Metabolism in Patients With Thalassemia Major

Who this might be right for
Thalassemia Major
National Taiwan University Hospital 100
Next Page