Not applicableUnknownNCT03198195What this trial is testingPost-transplant Cyclophosphamide in Wiskott-Aldrich SyndromeWho this might be right forWiskott-Aldrich Syndrome Capital Research Institute of Pediatrics 5
Testing effectiveness (Phase 2)Enrolling By InvitationNCT01852370What this trial is testingSequential Cadaveric Lung and Bone Marrow Transplant for Immune Deficiency DiseasesWho this might be right forSevere Combined Immunodeficiency (SCID)Immunodeficiency With Predominant T-cell Defect, UnspecifiedSevere Chronic Neutropenia+6 more Paul Szabolcs 16
Not applicableEnded earlyNCT00006054What this trial is testingAllogeneic Bone Marrow Transplantation in Patients With Primary ImmunodeficienciesWho this might be right forImmunologic Deficiency SyndromesChediak-Higashi SyndromeCommon Variable Immunodeficiency+11 more Fairview University Medical Center
Not applicableUnknownNCT00004341What this trial is testingStudy of Genetic and Molecular Defects in Primary Immunodeficiency DisordersWho this might be right forX-Linked AgammaglobulinemiaX-Linked Hyper IgM SyndromeWiskott-Aldrich Syndrome+1 more Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
Early research (Phase 1)Study completedNCT00774358What this trial is testingInterleukin-2 Treatment for Wiskott-Aldrich SyndromeWho this might be right forWiskott-Aldrich Syndrome (WAS)X-linked Thrombocytopenia Soma Jyonouchi 9
Not applicableStudy completedNCT04350164What this trial is testingRomiplostim Treatment for Thrombocytopenia in Patients With Wiskott-Aldrich Syndrome.Who this might be right forWiskott-Aldrich Syndrome Federal Research Institute of Pediatric Hematology, Oncology and Immunology 67
Not applicableStudy completedNCT05687474What this trial is testingBaby Detect : Genomic Newborn ScreeningWho this might be right forCongenital Adrenal HyperplasiaFamilial Hyperinsulinemic Hypoglycemia 1Phosphoglucomutase 1 Deficiency+121 more Centre Hospitalier Universitaire de Liege 6,824
Testing effectiveness (Phase 2)Study completedNCT01410825What this trial is testingPilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer for the Wiskott-Aldrich SyndromeWho this might be right forWiskott-Aldrich Syndrome David Williams 5
Not applicableStudy completedNCT04429568What this trial is testingTHC Crossover StudyWho this might be right forTHCCannabisCannabis Smoking+6 more University of California, San Francisco 14
Testing effectiveness (Phase 2)Ended earlyNCT00909363What this trial is testingThrombocytopenia and Bleeding in Wiskott-Aldrich Syndrome (WAS) PatientsWho this might be right forWiskott-Aldrich SyndromeThrombocytopeniaBleeding Weill Medical College of Cornell University 24
Testing effectiveness (Phase 2)Study completedNCT03513328What this trial is testingConditioning Regimen for Allogeneic Hematopoietic Stem-Cell TransplantationWho this might be right forBone Marrow Failure SyndromeThalassemiaSickle Cell Disease+13 more University of Florida 6
Testing effectiveness (Phase 2)Study completedNCT00730314What this trial is testingUnrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood CellsWho this might be right forSickle Cell DiseaseThalassemiaAnemia+9 more Children's Hospital Los Angeles 25
Testing effectiveness (Phase 2)Active Not RecruitingNCT01821781What this trial is testingImmune Disorder HSCT ProtocolWho this might be right forImmune Deficiency DisordersSevere Combined ImmunodeficiencyChronic Granulomatous Disease+11 more Washington University School of Medicine 20
Post-approval studies (Phase 4)Study completedNCT01289847What this trial is testingFind Out How Safe and Effective Gammaplex® is in Young People With Primary ImmunodeficiencyWho this might be right forPrimary Immune Deficiency DisordersCommon Variable ImmunodeficiencyX-linked Agammaglobulinemia+2 more Bio Products Laboratory 25
Testing effectiveness (Phase 2)Active Not RecruitingNCT02333760What this trial is testingLong Term Safety Follow up of Haematopoietic Stem Cell Gene Therapy for the Wiskott Aldrich SyndromeWho this might be right forWiskott-Aldrich Syndrome Genethon 10
Testing effectiveness (Phase 2)Study completedNCT01529827What this trial is testingFludarabine Phosphate, Melphalan, and Low-Dose Total-Body Irradiation Followed by Donor Peripheral Blood Stem Cell Transplant in Treating Patients With Hematologic MalignanciesWho this might be right forAccelerated Phase Chronic Myelogenous LeukemiaAdult Acute Lymphoblastic Leukemia in RemissionAdult Acute Myeloid Leukemia in Remission+75 more Roswell Park Cancer Institute 94
Not applicableUnknownNCT00006319What this trial is testingMolecular and Clinical Studies of Primary Immunodeficiency DiseasesWho this might be right forWiskott- Aldrich SyndromeADA Deficient SCID National Human Genome Research Institute (NHGRI) 266
Testing effectiveness (Phase 2)Study completedNCT01347242What this trial is testingGene Therapy for Wiskott-Aldrich Syndrome (WAS)Who this might be right forWiskott-Aldrich Syndrome Genethon 6
Not applicableActive Not RecruitingNCT01652092What this trial is testingAllogeneic Hematopoietic Stem Cell Transplant for Patients With Primary Immune DeficienciesWho this might be right forSCIDOmenn's SyndromeReticular Dysgenesis+11 more Masonic Cancer Center, University of Minnesota 57
Large-scale testing (Phase 3)Study completedNCT00220766What this trial is testingRapid Infusion of Immune Globulin Intravenous (Human) In Primary Immunodeficiency PatientsWho this might be right forImmunologic Deficiency SyndromeAgammaglobulinemiaSevere Combined Immunodeficiency+2 more Grifols Therapeutics LLC 100