Not applicableStudy completedNCT03399461What this trial is testingTargeted Literature Review and Subject Interviews in Wiskott-Aldrich Syndrome (WAS)Who this might be right forWiskott-Aldrich Syndrome GlaxoSmithKline 19
Testing effectiveness (Phase 2)Ended earlyNCT03333486What this trial is testingFludarabine Phosphate, Cyclophosphamide, Total Body Irradiation, and Donor Stem Cell Transplant in Treating Patients With Blood CancerWho this might be right forAccelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 PositiveAcute Leukemia in RemissionAcute Lymphoblastic Leukemia+34 more Roswell Park Cancer Institute 31
Not applicableStudy completedNCT00086476What this trial is testingStudy of Megakaryocytes From Patients With Abnormal Platelet VesiclesWho this might be right forBlood Coagulation Disorders National Human Genome Research Institute (NHGRI) 3
Post-approval studies (Phase 4)Study completedNCT00634569What this trial is testingSafety and Efficacy Study of Flebogamma 5% DIF IGIV in Pediatric SubjectsWho this might be right forPrimary Immune Deficiency Disease Instituto Grifols, S.A. 24
Testing effectiveness (Phase 2)UnknownNCT04371939What this trial is testingEfficacy and Safety of Romiplostim Versus Eltrombopag in the Treatment of Thrombocytopenia in Patients With Wiskott-Aldrich SyndromeWho this might be right forWiskott-Aldrich Syndrome Federal Research Institute of Pediatric Hematology, Oncology and Immunology 30
Early research (Phase 1)Study completedNCT01917708What this trial is testingBone Marrow Transplant With Abatacept for Non-Malignant DiseasesWho this might be right forHurler SyndromeFanconi AnemiaGlanzmann Thrombasthenia+12 more Emory University 10
Testing effectiveness (Phase 2)Looking for participantsNCT01962415What this trial is testingReduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCTWho this might be right forPrimary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+4 more Paul Szabolcs 100
Not applicableStudy completedNCT01953016What this trial is testingParticipation in a Research Registry for Immune DisordersWho this might be right forPrimary ImmunodeficienciesAPECEDCGD+2 more National Human Genome Research Institute (NHGRI) 716
Testing effectiveness (Phase 2)Study completedNCT01515462What this trial is testingGene Therapy for Wiskott-Aldrich SyndromeWho this might be right forWiskott-Aldrich Syndrome (WAS) Fondazione Telethon 8
Not applicableEnrolling By InvitationNCT07362407What this trial is testingAnalysis of the Therapeutic and Clinical Profile of Cannabinoid Treatments: A Real-World StudyWho this might be right forChronic PainDepression DisordersAnxiety Disorders+3 more Santa Catarina Federal University 384
Early research (Phase 1)Study completedNCT00160355What this trial is testingHaploidentical Hematopoietic Stem Cell Transplantation Patients With Wiskott-Aldrich SyndromeWho this might be right forWiskott-Aldrich Syndrome St. Jude Children's Research Hospital 4
Testing effectiveness (Phase 2)UnknownNCT03019809What this trial is testingA Trial of Plerixafor/G-CSF as Additional Agents for Conditioning Before TCR Alpha/Beta Depleted HSCT in WAS PatientsWho this might be right forWiskott-Aldrich SyndromeHematopoietic Stem Cell TransplantationGraft Failure Federal Research Institute of Pediatric Hematology, Oncology and Immunology 30
Not applicableLooking for participantsNCT04528355What this trial is testingData Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RICWho this might be right forPrimary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+2 more Paul Szabolcs 50
Large-scale testing (Phase 3)Study completedNCT00278954What this trial is testingEfficacy, Safety and Pharmacokinetics of Gammaplex in Primary Immunodeficiency Diseases.Who this might be right forPrimary ImmunodeficiencyCommon Variable HypogammaglobulinemiaX-linked Hypogammaglobulinemia+3 more Bio Products Laboratory 50
Testing effectiveness (Phase 2)Study completedNCT01347346What this trial is testingGene Therapy for WASWho this might be right forWiskott-Aldrich Syndrome Genethon 5
Early research (Phase 1)Study completedNCT00744692What this trial is testingReduced Intensity Conditioning for Umbilical Cord Blood Transplant in Pediatric Patients With Non-Malignant DisordersWho this might be right forNon Malignant DisordersImmunodeficienciesCongenital Marrow Failures+5 more Duke University 22
Testing effectiveness (Phase 2)Ended earlyNCT02512679What this trial is testingRelated Hematopoietic Stem Cell Transplantation (HSCT) for Genetic Diseases of Blood CellsWho this might be right forStem Cell TransplantationBone Marrow TransplantationPeripheral Blood Stem Cell Transplantation+10 more Children's Hospital Los Angeles 20
Large-scale testing (Phase 3)Active Not RecruitingNCT03837483What this trial is testingA Clinical Study to Evaluate the Use of a Cryopreserved Formulation of OTL-103 in Subjects With Wiskott-Aldrich SyndromeWho this might be right forWiskott-Aldrich Syndrome Fondazione Telethon 10
Testing effectiveness (Phase 2)Study completedNCT00919503What this trial is testingTreosulfan and Fludarabine Phosphate Before Donor Stem Cell Transplant in Treating Patients With Nonmalignant Inherited DisordersWho this might be right forNon-Neoplastic Hematologic and Lymphocytic Disorder Fred Hutchinson Cancer Center 98
Not applicableEnded earlyNCT01319851What this trial is testingAlefacept and Allogeneic Hematopoietic Stem Cell TransplantationWho this might be right forThalassemiaSickle Cell DiseaseGlanzmann Thrombasthenia+10 more Emory University 3