Testing effectiveness (Phase 2)Study completedNCT01347242What this trial is testingGene Therapy for Wiskott-Aldrich Syndrome (WAS)Who this might be right forWiskott-Aldrich Syndrome Genethon 6
Not applicableStudy completedNCT03399461What this trial is testingTargeted Literature Review and Subject Interviews in Wiskott-Aldrich Syndrome (WAS)Who this might be right forWiskott-Aldrich Syndrome GlaxoSmithKline 19
Testing effectiveness (Phase 2)UnknownNCT04371939What this trial is testingEfficacy and Safety of Romiplostim Versus Eltrombopag in the Treatment of Thrombocytopenia in Patients With Wiskott-Aldrich SyndromeWho this might be right forWiskott-Aldrich Syndrome Federal Research Institute of Pediatric Hematology, Oncology and Immunology 30
Testing effectiveness (Phase 2)Study completedNCT01410825What this trial is testingPilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer for the Wiskott-Aldrich SyndromeWho this might be right forWiskott-Aldrich Syndrome David Williams 5
Not applicableStudy completedNCT02064933What this trial is testingPatients Treated for Wiskott-Aldrich Syndrome (WAS) Since 1990Who this might be right forWiskott-Aldrich Syndrome National Institute of Allergy and Infectious Diseases (NIAID) 305
Testing effectiveness (Phase 2)Ended earlyNCT02512679What this trial is testingRelated Hematopoietic Stem Cell Transplantation (HSCT) for Genetic Diseases of Blood CellsWho this might be right forStem Cell TransplantationBone Marrow TransplantationPeripheral Blood Stem Cell Transplantation+10 more Children's Hospital Los Angeles 20
Post-approval studies (Phase 4)Study completedNCT01289847What this trial is testingFind Out How Safe and Effective Gammaplex® is in Young People With Primary ImmunodeficiencyWho this might be right forPrimary Immune Deficiency DisordersCommon Variable ImmunodeficiencyX-linked Agammaglobulinemia+2 more Bio Products Laboratory 25
Testing effectiveness (Phase 2)Study completedNCT00730314What this trial is testingUnrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood CellsWho this might be right forSickle Cell DiseaseThalassemiaAnemia+9 more Children's Hospital Los Angeles 25
Post-approval studies (Phase 4)Study completedNCT00634569What this trial is testingSafety and Efficacy Study of Flebogamma 5% DIF IGIV in Pediatric SubjectsWho this might be right forPrimary Immune Deficiency Disease Instituto Grifols, S.A. 24
Large-scale testing (Phase 3)Active Not RecruitingNCT03837483What this trial is testingA Clinical Study to Evaluate the Use of a Cryopreserved Formulation of OTL-103 in Subjects With Wiskott-Aldrich SyndromeWho this might be right forWiskott-Aldrich Syndrome Fondazione Telethon 10
Early research (Phase 1)Study completedNCT00774358What this trial is testingInterleukin-2 Treatment for Wiskott-Aldrich SyndromeWho this might be right forWiskott-Aldrich Syndrome (WAS)X-linked Thrombocytopenia Soma Jyonouchi 9
Testing effectiveness (Phase 2)Ended earlyNCT03333486What this trial is testingFludarabine Phosphate, Cyclophosphamide, Total Body Irradiation, and Donor Stem Cell Transplant in Treating Patients With Blood CancerWho this might be right forAccelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 PositiveAcute Leukemia in RemissionAcute Lymphoblastic Leukemia+34 more Roswell Park Cancer Institute 31
Early research (Phase 1)Study completedNCT01917708What this trial is testingBone Marrow Transplant With Abatacept for Non-Malignant DiseasesWho this might be right forHurler SyndromeFanconi AnemiaGlanzmann Thrombasthenia+12 more Emory University 10
Not applicableLooking for participantsNCT04528355What this trial is testingData Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RICWho this might be right forPrimary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+2 more Paul Szabolcs 50
Testing effectiveness (Phase 2)Study completedNCT00885833What this trial is testingStudy of Reduced Toxicity Myeloablative Conditioning Regimen for Wiskott-Aldrich Syndrome (WAS)Who this might be right forWiskott-Aldrich Syndrome The Korean Society of Pediatric Hematology Oncology 5
Testing effectiveness (Phase 2)Study completedNCT01529827What this trial is testingFludarabine Phosphate, Melphalan, and Low-Dose Total-Body Irradiation Followed by Donor Peripheral Blood Stem Cell Transplant in Treating Patients With Hematologic MalignanciesWho this might be right forAccelerated Phase Chronic Myelogenous LeukemiaAdult Acute Lymphoblastic Leukemia in RemissionAdult Acute Myeloid Leukemia in Remission+75 more Roswell Park Cancer Institute 94
Testing effectiveness (Phase 2)Study completedNCT01347346What this trial is testingGene Therapy for WASWho this might be right forWiskott-Aldrich Syndrome Genethon 5
Not applicableUnknownNCT03198195What this trial is testingPost-transplant Cyclophosphamide in Wiskott-Aldrich SyndromeWho this might be right forWiskott-Aldrich Syndrome Capital Research Institute of Pediatrics 5
Not applicableUnknownNCT00004341What this trial is testingStudy of Genetic and Molecular Defects in Primary Immunodeficiency DisordersWho this might be right forX-Linked AgammaglobulinemiaX-Linked Hyper IgM SyndromeWiskott-Aldrich Syndrome+1 more Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
Not applicableEnrolling By InvitationNCT07362407What this trial is testingAnalysis of the Therapeutic and Clinical Profile of Cannabinoid Treatments: A Real-World StudyWho this might be right forChronic PainDepression DisordersAnxiety Disorders+3 more Santa Catarina Federal University 384