Not applicableNo Longer AvailableNCT02233257What this trial is testingExpanded Access for Lorenzo's Oil (GTO/GTE) in AdrenoleukodystrophyWho this might be right forX-linked Adrenoleukodystrophy University of Minnesota
Not applicableUnknownNCT01927133What this trial is testingLIVER FIBROSIS PREVALENCE IN FRANCEWho this might be right forLiver Fibrosis Progression in Chronic Liver Disease Assistance Publique - Hôpitaux de Paris 10,000
Not applicableEnded earlyNCT04008849What this trial is testingA Follow-up Study in Patients With Inherited Metabolic Disorders (IMD) Who Underwent Hematopoietic Stem Cell Transplantation (HSCT) With MGTA-456Who this might be right forInherited Metabolic Disorders (IMD) Magenta Therapeutics, Inc. 3
Not applicableLooking for participantsNCT04880356What this trial is testingLongitudinal Study of Ultra-rare Inherited Metabolic and Degenerative Neurological Diseases.Who this might be right forInherited DiseaseRare DiseasesMetabolic Disease+3 more Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta 100
Early research (Phase 1)WithdrawnNCT02410239What this trial is testingMT2014-14 IT-MSC for Advanced Cerebral Adrenoleukodystrophy (cALD)Who this might be right forCerebral Adrenoleukodystrophy Masonic Cancer Center, University of Minnesota
Large-scale testing (Phase 3)Study completedNCT00007020What this trial is testingCompassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic AcidWho this might be right forInfantile Refsum's DiseaseZellweger SyndromeAdrenoleukodystrophy+2 more Mirum Pharmaceuticals, Inc. 85
Not applicableActive Not RecruitingNCT06304467What this trial is testingCM for Patients With ALD After Liver TransplantWho this might be right forAlcohol Use DisorderAlcohol; LiverPost Liver Transplant+2 more Arpan A. Patel, MD 30
Not applicableLooking for participantsNCT05939232What this trial is testingRegistry of X-linked AdrenoleukodystrophyWho this might be right forX-linked Adrenoleukodystrophy Beijing Tiantan Hospital 200
Not applicableStudy completedNCT03897634What this trial is testingRemote Microphone Candidacy StudyWho this might be right forHearing Loss, Sensorineural Northwestern University 22
Large-scale testing (Phase 3)Study completedNCT03852498What this trial is testingA Clinical Study to Assess the Efficacy and Safety of Gene Therapy for the Treatment of Cerebral Adrenoleukodystrophy (CALD)Who this might be right forCerebral Adrenoleukodystrophy (CALD) Genetix Biotherapeutics Inc. 35
Large-scale testing (Phase 3)Study completedNCT01838941What this trial is testingBetaine and Peroxisome Biogenesis DisordersWho this might be right forPeroxisome Biogenesis Disorders McGill University Health Centre/Research Institute of the McGill University Health Centre 12
Not applicableNot Yet RecruitingNCT07525258What this trial is testingImplementation Facilitation Pilot for Alcohol Use Disorder (AUD) in Alcohol-associated Liver Disease (ALD)Who this might be right forAlcohol Use DisorderAlcohol-associated Liver Disease Yale University 30
Large-scale testing (Phase 3)Study completedNCT02961803What this trial is testingMD1003-AMN MD1003 in AdrenomyeloneuropathyWho this might be right forAdrenomyeloneuropathyAdrenoleukodystrophyAMN MedDay Pharmaceuticals SA 67
Not applicableLooking for participantsNCT06796920What this trial is testingEpidural Spinal Cord Stimulation for Lower-limb Impairment in AdrenomyeloneuropathyWho this might be right forAdrenomyeloneuropathy Without Cerebral Involvement Third Military Medical University 10
Large-scale testing (Phase 3)Study completedNCT00176904What this trial is testingStem Cell Transplant for Inborn Errors of MetabolismWho this might be right forAdrenoleukodystrophyMetachromatic LeukodystrophyGloboid Cell Leukodystrophy+8 more Masonic Cancer Center, University of Minnesota 135
Testing effectiveness (Phase 2)WithdrawnNCT03196765What this trial is testingSafety, Pharmacokinetics and Pharmacodynamics of NV1205 in Pediatric Male Subjects With AdrenoleukodystrophyWho this might be right forX-Linked Adrenoleukodystrophy NeuroVia, Inc.
Large-scale testing (Phase 3)Looking for participantsNCT06461208What this trial is testingA PROspective Faecal MIcrobiota tranSplantation Trial to Improve outcomEs in Patients With CirrhosisWho this might be right forLiver Cirrhosis King's College London 300
Not applicableLooking for participantsNCT05699018What this trial is testingScreening in Primary Care of Advanced Liver Fibrosis in NAFLD And/or Alcoholic PatientsWho this might be right forNon-alcoholic Fatty Liver Disease (NAFLD)Alcoholic Liver Disease (ALD)Liver Fibrosis University Hospital, Angers 1,788
Early research (Phase 1)Temporarily pausedNCT06030648What this trial is testingMT2022-01: MSCs for ALDWho this might be right forCerebral Adrenoleukodystrophy Masonic Cancer Center, University of Minnesota 10
Large-scale testing (Phase 3)Looking for participantsNCT06513533What this trial is testingDimethyl Fumarate in AdrenomyeloneuropathyWho this might be right forAdrenomyeloneuropathy Without Cerebral Involvement Pujol, Aurora, M.D. 40