Large-scale testing (Phase 3)Active Not RecruitingNCT05627648What this trial is testingPhase 3 Study of KP-100LI in Subjects With Vocal Fold ScarWho this might be right forVocal Fold Scar Kringle Pharma, Inc. 62
Not applicableStudy completedNCT00244010What this trial is testingPartially Matched Stem Cell Transplantation for Patients With Refractory Severe Aplastic Anemia or Refractory CytopeniasWho this might be right forAnemia, AplasticAmegakaryocytic ThrombocytopeniaDiamond-Blackfan Anemia+1 more St. Jude Children's Research Hospital 4
Post-approval studies (Phase 4)Study completedNCT05759416What this trial is testingEvaluation Efficacy of Melatonin Gel as Adjunctive Therapy in Chronic PeriodontitisWho this might be right forChronic Periodontitis Al-Azhar University 40
Not applicableStudy completedNCT05687474What this trial is testingBaby Detect : Genomic Newborn ScreeningWho this might be right forCongenital Adrenal HyperplasiaFamilial Hyperinsulinemic Hypoglycemia 1Phosphoglucomutase 1 Deficiency+121 more Centre Hospitalier Universitaire de Liege 6,824
Not applicableUnknownNCT05495477What this trial is testingEffects of NIV and CPAP on Ventilation Distribution, Measured by EIT, During Deep Sedation in Paediatric PatientsWho this might be right forRespiratory FailureSedationMechanical Ventilation Complication Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico 20
Large-scale testing (Phase 3)UnknownNCT04475224What this trial is testingPhase 3 Study of KP-100IT in Subjects With Acute Spinal Cord InjuryWho this might be right forAcute Spinal Cord Injury Kringle Pharma, Inc. 25
Not applicableUnknownNCT03319888What this trial is testingEffect of CPAP in the Worsening of Renal Function in Early Stages of Chronic Kidney Disease (CKD)Who this might be right forChronic Kidney InsufficiencySleep Apnea Sociedad Española de Neumología y Cirugía Torácica 700
Large-scale testing (Phase 3)Study completedNCT00176852What this trial is testingStem Cell Transplant for HemoglobinopathyWho this might be right forSickle Cell DiseaseThalassemiaSevere Congenital Neutropenia+2 more Masonic Cancer Center, University of Minnesota 22
Not applicableStudy completedNCT00254059What this trial is testingStudy to Compare Polysomnography With Overnight Home Oximetry and Auto - CPAP for Sleep ApneaWho this might be right forObstructive Sleep Apnea University of British Columbia 60
Early research (Phase 1)Study completedNCT01917708What this trial is testingBone Marrow Transplant With Abatacept for Non-Malignant DiseasesWho this might be right forHurler SyndromeFanconi AnemiaGlanzmann Thrombasthenia+12 more Emory University 10
Testing effectiveness (Phase 2)Looking for participantsNCT07185256What this trial is testingSafety and Tolerability of Subretinally Injected OPGx-BEST1 in Patients With Best Vitelliform Macular Dystrophy (BVMD) or Autosomal-Recessive Bestrophinopathy (ARB)Who this might be right forARBBVMDAutosomal-Dominant Bestrophinopathy+1 more Opus Genetics, Inc 10
Testing effectiveness (Phase 2)UnknownNCT02061800What this trial is testingCD34+ (Malignant) Stem Cell Selection for Patients Receiving Allogenic Stem Cell TransplantWho this might be right forChronic Myeloid Leukemia (CML)Acute Myelogenous Leukemia (AML)Myelodysplastic Syndrome (MDS)+3 more Diane George 14
Not applicableEnrolling By InvitationNCT06696456What this trial is testingLong Term Follow-up Study of AAVAnc80-hOTOF Gene TherapyWho this might be right forOtoferlin Gene-mediated Hearing Loss Akouos, Inc. 30
Not applicableStudy completedNCT05621200What this trial is testingTranscranial Alternating Current Stimulation (tACS) in Patients With AtaxiaWho this might be right forAtaxiaSpinocerebellar AtaxiasMultiple System Atrophy+2 more Azienda Socio Sanitaria Territoriale degli Spedali Civili di Brescia 26
Testing effectiveness (Phase 2)Looking for participantsNCT05821959What this trial is testingGene Therapy Trial for Otoferlin Gene-mediated Hearing LossWho this might be right forSensorineural Hearing Loss, Bilateral Akouos, Inc. 22
Testing effectiveness (Phase 2)Study completedNCT01529827What this trial is testingFludarabine Phosphate, Melphalan, and Low-Dose Total-Body Irradiation Followed by Donor Peripheral Blood Stem Cell Transplant in Treating Patients With Hematologic MalignanciesWho this might be right forAccelerated Phase Chronic Myelogenous LeukemiaAdult Acute Lymphoblastic Leukemia in RemissionAdult Acute Myeloid Leukemia in Remission+75 more Roswell Park Cancer Institute 94
Testing effectiveness (Phase 2)Looking for participantsNCT06942572What this trial is testingA Phase 1/2, First-in-Human Dose Escalation/Expansion Study to Evaluate the Safety, Tolerability and Preliminary Efficacy of a Subretinal Injection of SB-007 in Subjects With Stargardt Disease (STGD1)Who this might be right forStargardt DiseaseStargardt Macular DegenerationStargardt Macular Dystrophy Splice Bio 57
Testing effectiveness (Phase 2)Enrolling By InvitationNCT06253507What this trial is testingPCCLCHIM-p47 (Lentiviral Vector Transduced CD34 Plus Cells) in Patients With p47 Autosomal Recessive Chronic Granulomatous Disease (AR-CGD)Who this might be right forp47Autosomal RecessiveChronic Granulomatous Disease National Institute of Allergy and Infectious Diseases (NIAID) 10
Not applicableStudy completedNCT05479656What this trial is testingA Rehabilitation Program to Increase Balance and Mobility in Ataxia of Charlevoix-SaguenayWho this might be right forAutosomal Recessive Spastic Ataxia of Charlevoix-Saguenay Élise Duchesne 10
Not applicableLooking for participantsNCT06967831What this trial is testingDrug Repurposing for Mitochondrial Disorders Using iPSCs Derived Neural CellsWho this might be right forLeigh Syndrome (Maternally Inherited, MILS)Leigh Syndrome (AR, AD, XR) Charite University, Berlin, Germany 80