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Results for “Ciliopathy”

356 trials

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Showing 20 of 356 results

Large-scale testing (Phase 3)Study completedNCT00426153
What this trial is testing

Octreotide in Severe Polycystic Liver Disease

Who this might be right for
Polycystic Kidney, Autosomal DominantPolycystic Liver DiseaseHepatomegaly+3 more
Mayo Clinic 42
Large-scale testing (Phase 3)WithdrawnNCT04786574
What this trial is testing

See if Tolvaptan Can Delay Dialysis in Infants and Children Who at Enrollment Are 28 Days to Less Than 12 Weeks Old With Autosomal Recessive Polycystic Kidney Disease (ARPKD)

Who this might be right for
Autosomal Recessive Polycystic Kidney Disease (ARPKD)
Otsuka Pharmaceutical Development & Commercialization, Inc.
Not applicableStudy completedNCT02250287
What this trial is testing

New Quantitive MRI Parameters in Assessing Kidneys of Autosomal Dominant Polycystic Kidney Disease

Who this might be right for
Autosomal Dominant Polycystic Kidney DiseaseKidney Disease
Mayo Clinic 20
Not applicableEnded earlyNCT00078091
What this trial is testing

Genetics and Clinical Characteristics of Bardet-Biedl Syndrome

Who this might be right for
Bardet-Biedl Syndrome
National Human Genome Research Institute (NHGRI) 194
Not applicableEnded earlyNCT00934791
What this trial is testing

Polycystic Liver Disease in Kidney Transplant

Who this might be right for
Polycystic Liver Disease
Mayo Clinic 2
Not applicableEnrolling By InvitationNCT06841224
What this trial is testing

The Factors Affecting IPP in Peritoneal Dialysis Patients with Polycystic Kidney Disease

Who this might be right for
Peritoneal DialysisPolycystic Kidney Diseases
Peking University First Hospital 30
Testing effectiveness (Phase 2)UnknownNCT01932450
What this trial is testing

Radiofrequency Ablation for ADPKD Blood Pressure and Disease Progression Control

Who this might be right for
Autosomal Dominant Polycystic Kidney DiseaseHypertension
Mei changlin 100
Not applicableStudy completedNCT04407481
What this trial is testing

PErfusioN, OxyGen ConsUmptIon and ENergetics in ADPKD (PENGUIN)

Who this might be right for
Polycystic Kidney Disease, AdultPolycystic Kidney, Autosomal Dominant
University of Colorado, Denver 22
Large-scale testing (Phase 3)Ended earlyNCT00920309
What this trial is testing

Rapamycin as Treatment for Autosomal Dominant Polycystic Kidney Disease (ADPKD): The Role of Biomarkers in Predicting a Response to Therapy

Who this might be right for
Autosomal Dominant Polycystic Kidney Disease
Yale University 21
Large-scale testing (Phase 3)Looking for participantsNCT07280585
What this trial is testing

STOP-PKD: SGLT2-inhibition to Improve Prognosis in Polycystic Kidney Disease

Who this might be right for
Polycystic Kidney, Autosomal Dominant
University of Cologne 420
Early research (Phase 1)Active Not RecruitingNCT04895748
What this trial is testing

DFF332 as a Single Agent and in Combination With Everolimus & Immuno-Oncology Agents in Advanced/Relapsed Renal Cancer & Other Malignancies

Who this might be right for
Carcinoma, Renal Cell
Novartis Pharmaceuticals 40
Not applicableStudy completedNCT06618209
What this trial is testing

Assessment of Oral Health Status of Children With Primary Ciliary Dyskinesia

Who this might be right for
Primary Ciliary DyskinesiaCaries,DentalQuality of Life+2 more
Marmara University 160
Testing effectiveness (Phase 2)Study completedNCT05190744
What this trial is testing

Probenecid (PB) to Treat Hereditary Nephrogenic Diabetes Insipidus (NDI), ADPKD Treated With Tolvaptan, and Severely Polyuric Patients With Previous Lithium Administration

Who this might be right for
Autosomal Dominant Polycystic Kidney DiseaseNephrogenic Diabetes InsipidusAcquired Nephrogenic Diabetes Insipidus+1 more
Mayo Clinic 36
Large-scale testing (Phase 3)Ended earlyNCT03184584
What this trial is testing

Open-Label Rollover Study of PBI 4050 in Subjects With Alström Syndrome

Who this might be right for
Alström Syndrome
Liminal BioSciences Ltd. 10
Early research (Phase 1)Not Yet RecruitingNCT06658964
What this trial is testing

Study to Evaluate the Drug-drug Interaction of JMKX003142 in Healthy Subjects

Who this might be right for
ADPKD (autosomal Dominant Polycystic Kidney Disease)
Jemincare 48
Not applicableLooking for participantsNCT05424016
What this trial is testing

Propranolol and Von Hippel-Lindau Disease

Who this might be right for
Hemangioblastoma of CNSVon Hippel-Lindau Disease
Assistance Publique - Hôpitaux de Paris 85
Testing effectiveness (Phase 2)Looking for participantsNCT05478083
What this trial is testing

A GnRH Agonist IN Pre-menopausal Women STudy to Treat Severe Polycystic Liver Disease

Who this might be right for
Polycystic Liver DiseaseAutosomal Dominant Polycystic Kidney
University Medical Center Groningen 36
Not applicableStudy completedNCT00970970
What this trial is testing

Visualizing Vascular Endothelial Growth Factor (VEGF) Producing Lesions in Von Hippel-Lindau Disease

Who this might be right for
Von Hippel-Lindau DiseaseHemangioblastomaRenal Cell Carcinoma+2 more
University Medical Center Groningen 22
Not applicableStudy completedNCT04858191
What this trial is testing

Utilizing Hyperpolarized 129Xe Magnetic Resonance Imaging in Children With Primary Ciliary Dyskinesia

Who this might be right for
Primary Ciliary Dyskinesia
The Hospital for Sick Children 16
Testing effectiveness (Phase 2)Study completedNCT02527863
What this trial is testing

Effect of the Aquaretic Tolvaptan on Nitric Oxide System

Who this might be right for
Autosomal Dominant Polycystic Kidney Disease
Regional Hospital Holstebro 18
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