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Results for “Congenital Bone Marrow Failure Syndromes”

206 trials

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Showing 20 of 206 results

Not applicableStudy completedNCT00521430
What this trial is testing

Donor Stem Cell Transplant After Conditioning Therapy in Treating Patients With Hematologic Cancer, Recurrent or Metastatic Solid Tumor, or Other Disease

Who this might be right for
LeukemiaLymphomaMultiple Myeloma and Plasma Cell Neoplasm+3 more
Asan Medical Center 30
Testing effectiveness (Phase 2)Active Not RecruitingNCT04069533
What this trial is testing

Lentiviral-mediated Gene Therapy for Pediatric Patients With Fanconi Anemia Subtype A

Who this might be right for
Fanconi Anemia Complementation Group A
Rocket Pharmaceuticals Inc. 7
Not applicableStudy completedNCT00005892
What this trial is testing

Study of Allogeneic Bone Marrow Transplantation Following Cyclophosphamide and Radiotherapy in Patients With Myelodysplastic Syndrome and Acute Leukemia Related to Fanconi's Anemia

Who this might be right for
Fanconi's AnemiaMyelodysplastic SyndromesLeukemia, Nonlymphocytic, Acute+1 more
Fairview University Medical Center
Testing effectiveness (Phase 2)Study completedNCT01362595
What this trial is testing

Pilot Phase I/II Study of Amino Acid Leucine in Treatment of Patients With Transfusion-Dependent Diamond Blackfan Anemia

Who this might be right for
Diamond Blackfan AnemiaBlackfan Diamond SyndromeDBA+2 more
Northwell Health 55
Testing effectiveness (Phase 2)Study completedNCT00479115
What this trial is testing

Mobilization and Collection of Peripheral Blood Stem Cells in Patients With Fanconi Anemia Using G-CSF and AMD3100

Who this might be right for
Fanconi Anemia
Children's Hospital Medical Center, Cincinnati 1
Early research (Phase 1)UnknownNCT03836690
What this trial is testing

Transfer of Effector Memory T Cells (Tem) Following Allogeneic Stem Cell Transplantation

Who this might be right for
LymphomaLeukemiaMyeloma+4 more
University College, London 18
Large-scale testing (Phase 3)Study completedNCT00235391
What this trial is testing

Expanded Access of Deferasirox to Patients With Congenital Disorders of Red Blood Cells and Chronic Iron Overload

Who this might be right for
ThalassemiaSickle Cell DiseaseDiamond Blackfan Anemia+1 more
Novartis Pharmaceuticals 1,683
Testing effectiveness (Phase 2)Study completedNCT02931071
What this trial is testing

Clinical Phase II Trial to Evaluate CD34+ Cells Mobilization and Collection in Patients With Fanconi Anemia for Subsequent Transduction With a Lentiviral Vector Carring FANCA Gene. FANCOSTEM-1

Who this might be right for
Fanconi Anemia
Hospital Universitari Vall d'Hebron Research Institute 13
Not applicableLooking for participantsNCT03050268
What this trial is testing

Familial Investigations of Childhood Cancer Predisposition

Who this might be right for
Acute LeukemiaAdenomatous PolyposisAdrenocortical Carcinoma+43 more
St. Jude Children's Research Hospital 1,500
Testing effectiveness (Phase 2)Looking for participantsNCT05796570
What this trial is testing

A Pilot Study to Evaluate the Feasibility of Post-Hematopoietic Stem Cell Transplant Prophylaxis With Decitabine Combined With Filgrastim for Children and Young Adults With AML, MDS and Related Myeloid Malignancies

Who this might be right for
Acute Myeloid LeukemiaMyelodysplastic SyndromesMyeloid Malignancies+4 more
Franziska Wachter 37
Not applicableLooking for participantsNCT06744283
What this trial is testing

Experience and Management of Cancer Screening-Related Anxiety in Fanconi Anemia

Who this might be right for
Fanconi Anemia
National Cancer Institute (NCI) 20
Post-approval studies (Phase 4)Study completedNCT00673608
What this trial is testing

Magnetic Resonance Imaging (MRI) Assessments of the Heart and Liver Iron Load in Patients With Transfusion Induced Iron Overload

Who this might be right for
HemoglobinopathiesMyelodysplastic SyndromesOther Inherited or Acquired Anaemia+4 more
Novartis 118
Large-scale testing (Phase 3)Study completedNCT00171821
What this trial is testing

A Study Assessing the Efficacy and Safety of Deferasirox in Patients With Transfusion-dependent Iron Overload

Who this might be right for
Transfusion-dependent Iron Overload
Novartis Pharmaceuticals 1,784
Not applicableLooking for participantsNCT06999954
What this trial is testing

Shwachman-Diamond Syndrome Global Patient Survey and Partnering Platform

Who this might be right for
Shwachman-Diamond SyndromeSDSIBMF+24 more
Shwachman-Diamond Syndrome Alliance Inc 8,000
Testing effectiveness (Phase 2)Study completedNCT02797977
What this trial is testing

A Phase 1/2 Trial SRA737 in Combination With Gemcitabine and Cisplatin or Gemcitabine Alone in Advanced Cancer Subjects

Who this might be right for
Advanced Solid Tumors
Sierra Oncology LLC - a GSK company 153
Not applicableNot Yet RecruitingNCT07005297
What this trial is testing

Clinical Genetics Branch Eligibility Screening Survey

Who this might be right for
MelanomaLi-Fraumeni SyndromePulmonary Blastoma+7 more
National Cancer Institute (NCI) 1,000
Large-scale testing (Phase 3)UnknownNCT06519786
What this trial is testing

Safety and Efficacy of Metformin for Treatment of Cytopenia in Children and Adolescents With Fanconi Anemia

Who this might be right for
Fanconi Anemia
Ain Shams University 30
Testing effectiveness (Phase 2)Study completedNCT00301834
What this trial is testing

Alemtuzumab, Fludarabine, and Busulfan Followed By Donor Stem Cell Transplant in Treating Young Patients With Hematologic Disorders

Who this might be right for
Congenital Amegakaryocytic ThrombocytopeniaDiamond-blackfan AnemiaLeukemia+2 more
University of California, San Francisco 35
Testing effectiveness (Phase 2)Study completedNCT02873975
What this trial is testing

LY2606368 (Prexasertib) in Patients With Solid Tumors With Replicative Stress or Homologous Repair Deficiency

Who this might be right for
Advanced Cancers
Dana-Farber Cancer Institute 27
Not applicableLooking for participantsNCT04781790
What this trial is testing

French National Registry of Bone Marrow Failures

Who this might be right for
Bone Marrow Failure Syndrome
Assistance Publique - Hôpitaux de Paris 5,000
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