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Results for “Congenital Bone Marrow Failure Syndromes”

204 trials

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Showing 20 of 204 results

Testing effectiveness (Phase 2)UnknownNCT02386267
What this trial is testing

L-leucine in Diamond Blackfan Anemia Patients

Who this might be right for
Diamond Blackfan Anemia
Federal Scientific Clinical Centre of Pediatric Hematology, Oncology and Immunology named after Dmitry Rogache 30
Testing effectiveness (Phase 2)Study completedNCT02797977
What this trial is testing

A Phase 1/2 Trial SRA737 in Combination With Gemcitabine and Cisplatin or Gemcitabine Alone in Advanced Cancer Subjects

Who this might be right for
Advanced Solid Tumors
Sierra Oncology LLC - a GSK company 153
Testing effectiveness (Phase 2)Study completedNCT00600938
What this trial is testing

Evaluating Use of Deferasirox as Compared to Deferoxamine in Treating Cardiac Iron Overload

Who this might be right for
Transfusional Iron OverloadTransfusional Hemosiderosis
Novartis Pharmaceuticals 197
Not applicableLooking for participantsNCT05012111
What this trial is testing

Natural History of Acquired and Inherited Bone Marrow Failure Syndromes

Who this might be right for
Severe Aplastic AnemiaTelomere Biology DisordersInherited Bone Marrow Failure Syndromes
National Heart, Lung, and Blood Institute (NHLBI) 1,000
Not applicableLooking for participantsNCT04645199
What this trial is testing

National Longitudinal Cohort of Hematological Diseases

Who this might be right for
Multiple MyelomaAcute Myeloid LeukemiaHemophilia+14 more
Institute of Hematology & Blood Diseases Hospital, China 2,300
Not applicableStudy completedNCT03609814
What this trial is testing

Study of Clofarabine and Fludarabine Drug Exposure in Pediatric Bone Marrow Transplantation (HCT)

Who this might be right for
Hematologic MalignanciesNonmalignant DiseasesImmunodeficiencies+5 more
University of California, San Francisco 30
Testing effectiveness (Phase 2)Active Not RecruitingNCT03206086
What this trial is testing

Eltrombopag for People With Fanconi Anemia

Who this might be right for
Fanconi Anemia
National Heart, Lung, and Blood Institute (NHLBI) 25
Testing effectiveness (Phase 2)Ended earlyNCT02512679
What this trial is testing

Related Hematopoietic Stem Cell Transplantation (HSCT) for Genetic Diseases of Blood Cells

Who this might be right for
Stem Cell TransplantationBone Marrow TransplantationPeripheral Blood Stem Cell Transplantation+10 more
Children's Hospital Los Angeles 20
Not applicableLooking for participantsNCT01137643
What this trial is testing

Tissue, Blood, and Body Fluid Sample Collection From Patients With Hematologic Cancer

Who this might be right for
Chronic Myeloproliferative DisordersLeukemiaLymphoma+5 more
UNC Lineberger Comprehensive Cancer Center 15,000
Not applicableStudy completedNCT00964821
What this trial is testing

Flu Vaccine in Preventing Influenza Infection in Healthy Volunteers and in Patients Who Have Undergone Stem Cell Transplant

Who this might be right for
Chronic Myeloproliferative DisordersLeukemiaLymphoma+4 more
City of Hope Medical Center 459
Testing effectiveness (Phase 2)Study completedNCT02797964
What this trial is testing

A Phase 1/2 Trial of SRA737 in Subjects With Advanced Cancer

Who this might be right for
Advanced Solid Tumors or Non-Hodgkin's Lymphoma (NHL)
Sierra Oncology LLC - a GSK company 107
Not applicableStudy completedNCT00521430
What this trial is testing

Donor Stem Cell Transplant After Conditioning Therapy in Treating Patients With Hematologic Cancer, Recurrent or Metastatic Solid Tumor, or Other Disease

Who this might be right for
LeukemiaLymphomaMultiple Myeloma and Plasma Cell Neoplasm+3 more
Asan Medical Center 30
Not applicableAvailableNCT01995305
What this trial is testing

Use Massive Parallel Sequencing and Exome Capture Technology to Sequence the Exome of Fanconi Anemia Children and Their Patents

Who this might be right for
Fanconi AnemiaAutosomal or Sex Linked Recessive Genetic DiseaseBone Marrow Hematopoiesis Failure, Multiple Congenital Abnormalities, and Susceptibility to Neoplastic Diseases.+1 more
Xiaofan Zhu
Not applicableLooking for participantsNCT04781790
What this trial is testing

French National Registry of Bone Marrow Failures

Who this might be right for
Bone Marrow Failure Syndrome
Assistance Publique - Hôpitaux de Paris 5,000
Testing effectiveness (Phase 2)Looking for participantsNCT05796570
What this trial is testing

A Pilot Study to Evaluate the Feasibility of Post-Hematopoietic Stem Cell Transplant Prophylaxis With Decitabine Combined With Filgrastim for Children and Young Adults With AML, MDS and Related Myeloid Malignancies

Who this might be right for
Acute Myeloid LeukemiaMyelodysplastic SyndromesMyeloid Malignancies+4 more
Franziska Wachter 37
Testing effectiveness (Phase 2)Active Not RecruitingNCT04248439
What this trial is testing

Gene Therapy for Fanconi Anemia, Complementation Group A

Who this might be right for
Fanconi Anemia Complementation Group A
Rocket Pharmaceuticals Inc. 5
Not applicableLooking for participantsNCT07205523
What this trial is testing

High-Altitude Hematology Observation-Stem Cell Transplantation (HALO-SCT)

Who this might be right for
Hematopoietic Stem Cell Transplantation (HSCT)Acute Myeloid Leukemia (AML)Leukemias, Acute Myeloid+12 more
Yigeng Cao,MD,PhD 1,000
Testing effectiveness (Phase 2)Active Not RecruitingNCT01659606
What this trial is testing

Radiation- and Alkylator-free Bone Marrow Transplantation Regimen for Patients With Dyskeratosis Congenita

Who this might be right for
Dyskeratosis CongenitaHoyeraal Hreidarsson SyndromeRevesz Syndrome+1 more
Boston Children's Hospital 40
Not applicableEnded earlyNCT04275479
What this trial is testing

Diabetes/ Endocrine Surveillance in SDS

Who this might be right for
Shwachman-Diamond Syndrome
Washington University School of Medicine 11
Not applicableStudy completedNCT06490510
What this trial is testing

Prognostic Significance of Mutation Type and Chromosome Fragility in Fanconi Anemia

Who this might be right for
Fanconi Anemia
Fundació Institut de Recerca de l'Hospital de la Santa Creu i Sant Pau 227
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