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Results for “Congenital Hematological Disorder”

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Showing 20 of 0 results

Not applicableUnknownNCT05434728
What this trial is testing

Characterization of Bleeding Disorders in EDS

Who this might be right for
Ehlers-Danlos SyndromeEDSClassical Ehlers-Danlos Syndrome+5 more
University Health Network, Toronto 45
Testing effectiveness (Phase 2)Study completedNCT04218071
What this trial is testing

Actuate 1901: 9-ING-41 in Myelofibrosis

Who this might be right for
Myelofibrosis
Actuate Therapeutics Inc. 17
Not applicableNot Yet RecruitingNCT07474428
What this trial is testing

Quality of Life in Pediatric Participants With HHT

Who this might be right for
Hereditary Haemorrhagic Telangiectasia (HHT)
Ashley Nelson 70
Testing effectiveness (Phase 2)Ended earlyNCT02757911
What this trial is testing

Gene Therapy for X-linked Chronic Granulomatous Disease

Who this might be right for
X-Linked Chronic Granulomatous Disease
Genethon 3
Testing effectiveness (Phase 2)Study completedNCT03476330
What this trial is testing

Quercetin Chemoprevention for Squamous Cell Carcinoma in Patients With Fanconi Anemia

Who this might be right for
Fanconi AnemiaSquamous Cell Carcinoma
Children's Hospital Medical Center, Cincinnati 48
Testing effectiveness (Phase 2)Study completedNCT00006136
What this trial is testing

Phase II Study of Arginine Butyrate With or Without Epoetin Alfa in Patients With Thalassemia Intermedia

Who this might be right for
Beta-Thalassemia
Boston University 15
Not applicableStudy completedNCT02638012
What this trial is testing

Prospective Pilot Study of Floseal for the Treatment of Anterior Epistaxis in Patients With (HHT)

Who this might be right for
Hereditary Hemorrhagic Telangiectasia (HHT)Epistaxis
Unity Health Toronto 8
Testing effectiveness (Phase 2)Study completedNCT00901199
What this trial is testing

Combined Chelation Therapy in Patients With Transfusion Dependent Thalassemia and Iron Overload

Who this might be right for
ThalassemiaIron Overload
Elliott Vichinsky 22
Not applicableUnknownNCT02199639
What this trial is testing

Transcultural Multidisciplinary Evaluation of Patients With Hemophili

Who this might be right for
Patients With Haemophilia
Universidad Católica San Antonio de Murcia 100
Testing effectiveness (Phase 2)Study completedNCT00089011
What this trial is testing

Tacrolimus and Mycophenolate Mofetil in Preventing Graft-Versus-Host Disease in Patients Who Have Undergone Total-Body Irradiation With or Without Fludarabine Phosphate Followed by Donor Peripheral Blood Stem Cell Transplant for Hematologic Cancer

Who this might be right for
Accelerated Phase Chronic Myelogenous LeukemiaAdult Acute Lymphoblastic Leukemia in RemissionAdult Acute Myeloid Leukemia in Remission+171 more
Fred Hutchinson Cancer Center 150
Not applicableNot Yet RecruitingNCT06619093
What this trial is testing

Relationship Between Biological Phenotype, Clinical Severity of Sickle Cell Disease, and Blood Coagulation

Who this might be right for
Sickle Cell Disease (SCD)
Hospices Civils de Lyon 200
Not applicableNot Yet RecruitingNCT07830693
What this trial is testing

Efanesoctocog Prophylaxis Or The Optimization Of Treatment: Real-World Experience Of Taylorizing Clotting Therapy In Hemophilia A

Who this might be right for
Hemophilia A Patient
Nantes University Hospital 553
Early research (Phase 1)Ended earlyNCT02049801
What this trial is testing

MEK Inhibitor MEK162, Idarubicin, and Cytarabine in Treating Patients With Relapsed or Refractory Acute Myeloid Leukemia

Who this might be right for
Adult Acute Minimally Differentiated Myeloid Leukemia (M0)Adult Acute Monoblastic Leukemia (M5a)Adult Acute Monocytic Leukemia (M5b)+12 more
Bruno C. Medeiros 1
Not applicableUnknownNCT03171909
What this trial is testing

Austrian Registry on the Outcome of Monochorionic Pregnancies

Who this might be right for
Twin Dichorionic Diamniotic PlacentaTwin Monochorionic Monoamniotic PlacentaTwin-To-Twin Transfusion Syndrome+1 more
Medical University of Graz 1,000
Large-scale testing (Phase 3)Study completedNCT01125254
What this trial is testing

Amlodipine Use in the Prevention and Treatment of Iron Overload in Patients With Thalassemia Major

Who this might be right for
Thalassemia Major
University of Campinas, Brazil 10
Post-approval studies (Phase 4)WithdrawnNCT04690322
What this trial is testing

POCUS: Hemostatic Potential and Joint Health in Patients With Severe Hemophilia A on Novel Replacement Therapies

Who this might be right for
Hemophilia AFactor VIII
University of Texas Southwestern Medical Center
Testing effectiveness (Phase 2)Study completedNCT00777231
What this trial is testing

Phase I/II Pilot Study of Mixed Chimerism to Treat Hemoglobinopathies

Who this might be right for
Sickle Cell Disease
Talaris Therapeutics Inc. 9
Not applicableStudy completedNCT00230672
What this trial is testing

Investigation of Plasma Proteins in Patients With Hereditary Haemorrhagic Telangiectasia and PAVMs

Who this might be right for
Telangiectasia, Hereditary Hemorrhagic
Imperial College London 1
Not applicableEnded earlyNCT03603275
What this trial is testing

Assessing Physician and Hemophilia A Patient Reasons and Expectations for Switching Treatment to Kovaltry & Jivi: A Nested Study Within an Existing Registry

Who this might be right for
Hemophilia A
Bayer 3
Not applicableStudy completedNCT04892628
What this trial is testing

Effects of Progressive Resistance Training Compared With Aerobic Training in Patients With Hemophilia

Who this might be right for
Quality of LifeMuscle Weakness
Dow University of Health Sciences 60
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