Not applicableStudy completedNCT02212314What this trial is testingResponse Inhibition Training for Children With Williams SyndromeWho this might be right forWilliams Syndrome University of Wisconsin, Milwaukee 25
Large-scale testing (Phase 3)Ended earlyNCT01583114What this trial is testingPREclinical Mutation CARriers From Families With DIlated Cardiomyopathy and ACE InhibitorsWho this might be right forDilated Cardiomyopathy Institut National de la Santé Et de la Recherche Médicale, France 6
Not applicableStudy completedNCT05155865What this trial is testingConduction System Pacing Versus Biventricular Pacing for Cardiac ResYNChronizationWho this might be right forDilated Cardiomyopathy with Conduction DefectLeft Bundle-Branch BlockHeart Failure+2 more University Medical Centre Ljubljana 62
Not applicableStudy completedNCT01585831What this trial is testingStudy of Psychological and Motor Effects of Testosterone in Adolescents With XXY/Klinefelter SyndromeWho this might be right forKlinefelter SyndromeXXY Syndrome University of Colorado, Denver 48
Large-scale testing (Phase 3)Study completedNCT03843541What this trial is testingA Clinical Trial to Compare the Efficacy and Safety of 1-week Treatment of Intravenous N-acetylcysteine (NAC) 600 mg Twice Daily, Ambroxol Hydrochloride 30 mg Twice Daily and Placebo as Expectorant Therapies in Adult Chinese Patients With Respiratory Tract Diseases and Abnormal Mucus SecretionsWho this might be right forRespiratory Tract DiseasesAbnormal Mucus Secretions Zambon SpA 333
Testing effectiveness (Phase 2)Study completedNCT01525875What this trial is testingMagnesium Supplements In The Treatment Of Pseudoxanthoma Elasticum (PXE)Who this might be right forPseudoxanthoma Elasticum Mark Lebwohl 44
Early research (Phase 1)Ended earlyNCT06597656What this trial is testingA Gene Transfer Therapy to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) Following Therapeutic Plasma Exchange (Plasmapheresis) in Participants With Duchenne Muscular Dystrophy (DMD) and Pre-existing Antibodies to AAVrh74Who this might be right forDuchenne Muscular Dystrophy Sarepta Therapeutics, Inc. 3
Early research (Phase 1)WithdrawnNCT06483802What this trial is testingASP2016 in Adults Who Have Heart Disease Associated With Friedreich AtaxiaWho this might be right forFriedreich AtaxiaCardiomyopathy Astellas Gene Therapies
Early research (Phase 1)Study completedNCT06673654What this trial is testingA Study, Comparing Ruxolitinib Topical Cream 1.5% (Taro Pharmaceuticals U.S.A, Inc.) to OPZELURA (Ruxolitinib) Cream for the Treatment of Mild-to-Moderate Atopic Dermatitis.Who this might be right forAtopic Dermatitis Sun Pharmaceutical Industries, Inc. 476
Testing effectiveness (Phase 2)Study completedNCT03489629What this trial is testingSTaph Aureus Resistance-Treat Early and Repeat (STAR-TER)Who this might be right forCystic Fibrosis University of North Carolina, Chapel Hill 49
Not applicableStudy completedNCT01974830What this trial is testingAL1TER™: Alpha-1 Therapy, Evaluation, and Research Patient RegistryWho this might be right forAlpha-1 Anti-trypsin Deficiency Coram Clinical Trials 120
Not applicableStudy completedNCT04458766What this trial is testingThe Use of Mobile Health Technology and Behavioral Economics to Encourage Adherence in AdolescentsWho this might be right forFamilial HypercholesterolemiaAdherence, Medication Boston Children's Hospital 11
Not applicableStudy completedNCT02830477What this trial is testingStudy Evaluating "Real World" Treatment Pattern in Previously Treated Hemophilia A Patients Receiving KOVALTRY (Octocog Alfa) for Routine ProphylaxisWho this might be right forHemophilia A, Congenital Bayer 313
Testing effectiveness (Phase 2)Study completedNCT02536170What this trial is testingArginine Therapy for Sickle Cell Disease PainWho this might be right forSickle Cell DiseaseVaso-occlusive Pain Episode Emory University 108
Testing effectiveness (Phase 2)Study completedNCT04284657What this trial is testingPravastatin and Alkali Therapy in Patients With Autosomal Dominant Polycystic Kidney DiseaseWho this might be right forAutosomal Dominant Polycystic Kidney Disease University of Southern California 1
Large-scale testing (Phase 3)Study completedNCT02987257What this trial is testingNATIENS: Optimal Management and Mechanisms of SJS/TENWho this might be right forStevens-Johnson SyndromeToxic Epidermal Necrolyses Vanderbilt University Medical Center 2
Not applicableStudy completedNCT03664167What this trial is testingWeight Loss for Obese Individuals With GoutWho this might be right forGout, Arthritis, Obesity Henning Bliddal 60
Testing effectiveness (Phase 2)Active Not RecruitingNCT06421636What this trial is testingTest the Safety, Tolerability, and Efficacy of an Antibody, REGN7999, Injected Under the Skin for the Treatment of Iron Overload in Adult Participants With Non-Transfusion Dependent β-thalassemia, Using MRI Scans to Measure Iron Levels in the BodyWho this might be right forNon-Transfusion Dependent Beta-Thalassemia (NTDT) Regeneron Pharmaceuticals 19
Early research (Phase 1)WithdrawnNCT05158439What this trial is testingSafety of Cultured Allogeneic Adult Umbilical Cord Derived Mesenchymal Stem Cells for Tourette SyndromeWho this might be right forTourette Syndrome The Foundation for Orthopaedics and Regenerative Medicine
Testing effectiveness (Phase 2)Active Not RecruitingNCT06390865What this trial is testingTesting MLN0128 (TAK-228) as Potentially Targeted Treatment in Cancers With TSC1 or TSC2 Genetic Changes (MATCH - Subprotocol M)Who this might be right forAdvanced LymphomaAdvanced Malignant Solid NeoplasmRefractory Lymphoma+2 more National Cancer Institute (NCI) 49