Not applicableStudy completedNCT06054971What this trial is testingNSAA NON-Interventional Study ProtocolWho this might be right forDuchenne Muscular Dystrophy Red Nucleus Enterprise Solutions, LLC 31
Testing effectiveness (Phase 2)Looking for participantsNCT06844214What this trial is testingInvestigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1Who this might be right forMyotonic Dystrophy Sanofi 32
Testing effectiveness (Phase 2)Ended earlyNCT01239758What this trial is testingExtension Study of ACE-031 in Subjects With Duchenne Muscular DystrophyWho this might be right forDuchenne Muscular Dystrophy Acceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway, NJ USA 11
Not applicableLooking for participantsNCT07515235What this trial is testingDMD Gene Variants and Cardiac Dysfunction in Young Males With DystrophinopathiesWho this might be right forDuchenne Muscular Dystrophy (DMD)Becker Muscular DystrophyCardiomyopathy Aristotle University Of Thessaloniki 65
Large-scale testing (Phase 3)Study completedNCT01197300What this trial is testing1 Year Open-label Extension to CZOL446H2337 Safety and Efficacy Trial of Zoledronic Acid Twice Yearly in Osteoporotic Children Treated With GlucocorticoidsWho this might be right forOsteoporosis Novartis Pharmaceuticals 25
Not applicableNot Yet RecruitingNCT07368400What this trial is testingDMD and Gamified PhysiotherapyWho this might be right forDuchenne Muscular Dystrophy (DMD) Başak Çağla Arslan 46
Not applicableStudy completedNCT02034305What this trial is testingPeak Cough Flow and Cough Clearance in Patients With Muscular DystrophyWho this might be right forDuchenne Muscular Dystrophy University of Pittsburgh 7
Not applicableStudy completedNCT05916677What this trial is testingVirtual Reality-training in Theory of Mind in the Childhood Form of Myotonic Dystrophy Type 1Who this might be right forMyotonic Dystrophy Type 1 Institut de Myologie, France 35
Not applicableEnrolling By InvitationNCT06605612What this trial is testingDevelopment and Validation of the FBIndex to Determine the Risk of Falls for Patients With Neuromuscular DisordersWho this might be right forInclusion Body MyositisMyotonic DystrophyLimb-girdle and Facioscapulohumeral Muscular Dystrophies+9 more LMU Klinikum 108
Testing effectiveness (Phase 2)Study completedNCT04322357What this trial is testingTwice Weekly Steroids and Exercise as Therapy for DMDWho this might be right forDuchenne Muscular Dystrophy (DMD) University of Florida 21
Large-scale testing (Phase 3)Study completedNCT01826487What this trial is testingPhase 3 Study of Ataluren in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)Who this might be right forMuscular Dystrophy, DuchenneMuscular DystrophiesMuscular Disorders, Atrophic+6 more PTC Therapeutics 230
Not applicableStudy completedNCT00094393What this trial is testingClinical Studies of ProgeriaWho this might be right forProgeria National Human Genome Research Institute (NHGRI) 15
Large-scale testing (Phase 3)Study completedNCT05096221What this trial is testingA Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)Who this might be right forDuchenne Muscular Dystrophy Sarepta Therapeutics, Inc. 126
Post-approval studies (Phase 4)Ended earlyNCT04708314What this trial is testingAn Open-Label Study of Golodirsen in Non-Ambulant Patients With Duchenne Muscular DystrophyWho this might be right forDuchenne Muscular Dystrophy Rare Disease Research, LLC 2
Not applicableStudy completedNCT00893334What this trial is testingEvaluation of Limb-Girdle Muscular DystrophyWho this might be right forBecker Muscular DystrophyLimb-Girdle Muscular Dystrophy, Type 2A (Calpain-3 Deficiency)Limb-Girdle Muscular Dystrophy, Type 2B (Miyoshi Myopathy, Dysferlin Deficiency)+1 more Cooperative International Neuromuscular Research Group 60
Not applicableStudy completedNCT02375087What this trial is testingSleep Breathing Disorders, a Main Trigger for Cardiac ARythmias in Type I Myotonic Dystrophy ?Who this might be right forMyotonic Dystrophy University Hospital, Grenoble 73
Testing effectiveness (Phase 2)Looking for participantsNCT06300307What this trial is testingStudy of ATX-01 in Participants With DM1Who this might be right forMyotonic Dystrophy 1 ARTHEx Biotech S.L. 56
Testing effectiveness (Phase 2)Study completedNCT00102453What this trial is testingPentoxifylline in Duchenne Muscular DystrophyWho this might be right forMuscular Dystrophy, Duchenne Cooperative International Neuromuscular Research Group 17
Testing effectiveness (Phase 2)UnknownNCT02285673What this trial is testingEfficacy of Umbilical Cord Mesenchymal Stem Cells in Duchenne Muscular DystrophyWho this might be right forDuchenne Muscular Dystrophy Acibadem University 10
Not applicableNot Yet RecruitingNCT07475754What this trial is testingEvaluate the Safety and Tolerability of Rituxan in Duchenne Muscular DystrophyWho this might be right forDuchenne Muscular Dystrophy (DMD) Peking Union Medical College Hospital 5