Not applicableStudy completedNCT02113917What this trial is testingChildren and Adult Hemophagocytic Syndrome (HLHa)Who this might be right forHemophagocytic Syndrome Assistance Publique - Hôpitaux de Paris 204
Not applicableUnknownNCT02000310What this trial is testingMolecular and Cellular Mechanisms of Lysosomal Storage DiseasesWho this might be right forLysosomal Storage Disorders O & O Alpan LLC 80
Testing effectiveness (Phase 2)Active Not RecruitingNCT02523040What this trial is testingLenalidomide for Adult Histiocyte DisordersWho this might be right forLangerhans Cell Histiocytosis (LCH)Histiocytoses Erdheim-chester DiseaseHistiocytic Sarcoma (HS) Dana-Farber Cancer Institute 12
Post-approval studies (Phase 4)Not Yet RecruitingNCT06504030What this trial is testingModified DEP Regimens for the Treatment of Hemophagocytic LymphohistiocytosisWho this might be right forHemophagocytic Lymphohistiocytoses The First Affiliated Hospital of Soochow University 20
Large-scale testing (Phase 3)UnknownNCT02862054What this trial is testingSplenectomy as a Treatment for Patient With Relapsed Haemophagocytic Lymphohistiocytosis of Unknown EtiologyWho this might be right forHemophagocytic Lymphohistiocytosis Beijing Friendship Hospital 30
Not applicableUnknownNCT05914727What this trial is testingBiomarkers Of Lung InVolvement In ASMDWho this might be right forAsmd, Visceral Type Eline C. B. Eskes 68
Post-approval studies (Phase 4)Study completedNCT05744063What this trial is testingA Post-authorization Study to Describe the Safety and Efficacy of Emapalumab for the Treatment of pHLH in Treatment Experienced Chinese PatientsWho this might be right forPrimary Hemophagocytic Lymphohistiocytosis Swedish Orphan Biovitrum 13
Not applicableLooking for participantsNCT03990428What this trial is testingSupportive Care Needs of Caregivers of People With Erdheim-Chester Disease and Other Histiocytic DiseasesWho this might be right forSupportive Care Needs of Caregivers Memorial Sloan Kettering Cancer Center 250
Not applicableNot Yet RecruitingNCT06491719What this trial is testingA Study on Efficacy and Safety of iNK Cells for CAEBV /EBV-HLH After Allo-HSCTWho this might be right forCAEBV (Chronic Active Epstein-Barr Virus Infection) SyndromeEBVHemophagocytic Lymphohistiocytoses Beijing Friendship Hospital 15
Not applicableLooking for participantsNCT03333200What this trial is testingLongitudinal Study of Neurodegenerative DisordersWho this might be right forMLDKrabbe DiseaseALD+24 more University of Pittsburgh 1,500
Not applicableStudy completedNCT04845958What this trial is testingA Non-Interventional National Study in Pediatric Patients With Unexplained Enlarged SpleenWho this might be right forGaucher Disease, SplenomegalyAcid SphingoMyelinase Deficiency Sanofi 60
Large-scale testing (Phase 3)UnknownNCT04077905What this trial is testingPegylated Liposomal Doxorubicin as a Induction Therapy for Lymphoma Induced Hemophagocytic Lymphohistiocytosis.Who this might be right forHemophagocytic Lymphohistiocytosis Beijing Friendship Hospital 160
Testing effectiveness (Phase 2)Looking for participantsNCT05828069What this trial is testingA Study With Tovorafenib (DAY101) as a Treatment Option for Progressive, Relapsed, or Refractory Langerhans Cell HistiocytosisWho this might be right forRecurrent Langerhans Cell HistiocytosisRefractory Langerhans Cell Histiocytosis National Cancer Institute (NCI) 48
Not applicableUnknownNCT00006056What this trial is testingPilot Study of Unrelated Donor Hematopoietic Stem Cell Transplantation in Patients With Life Threatening Hemophagocytic DisordersWho this might be right forChediak-Higashi SyndromeGraft Versus Host DiseaseX-Linked Lymphoproliferative Syndrome+3 more Fairview University Medical Center 40
Not applicableUnknownNCT05904366What this trial is testingMagnetic Resonance Spectroscopy in Acid Sphingomyelinase DeficiencyWho this might be right forAsmd, Visceral Type Eline C. B. Eskes 34
Not applicableEnrolling By InvitationNCT03655223What this trial is testingEarly Check: Expanded Screening in NewbornsWho this might be right forSpinal Muscular AtrophyFragile X SyndromeFragile X - Premutation+182 more RTI International 30,000
Large-scale testing (Phase 3)Looking for participantsNCT04943211What this trial is testingDetermination of Molecular Status, the Efficacy and Safety of Fluorodeoxyglucose in PET-CT ImagingWho this might be right forHistiocytosis Anna Raciborska 150
Not applicableActive Not RecruitingNCT05236764What this trial is testingHaploidentical Hematopoietic Cell Transplantation Using TCR Alpha/Beta and CD19 DepletionWho this might be right forAcute Lymphoblastic Leukemia in RemissionAcute Myeloid Leukemia in RemissionMyelodysplastic Syndromes+8 more Baylor College of Medicine 3
Testing effectiveness (Phase 2)Looking for participantsNCT04079179What this trial is testingCobimetinib in Refractory Langerhans Cell Histiocytosis (LCH), and Other Histiocytic DisordersWho this might be right forLangerhan's Cell HistiocytosisJuvenile XanthogranulomaErdheim-Chester Disease+4 more Carl Allen 90
Not applicableStudy completedNCT02435030What this trial is testingA Prospective Non-therapeutic Study in Patients Diagnosed With Niemann-Pick Disease Type CWho this might be right forNiemann-Pick Disease, Type C ZevraDenmark 35