Crick
HomeTrialsGenesDrugs23andMeGraphBlogContact
  • Home
  • Trials
  • Genes
  • Drugs
  • 23andMe
  • Graph
  • Blog
  • Contact
Crick

An open-source clinical intelligence platform. Explore clinical trials, gene networks, and molecular structures using public data sources.

Data Sources

  • ClinicalTrials.gov
  • OpenTargets
  • ClinVar
  • PubChem

Links

  • Contact
  • About
  • Privacy

© 2026 Crick. All rights reserved.

Crick is for educational purposes only. Not medical advice.

Results for “Inherited BMF Syndrome”

152 trials

Filters

Phase
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Status
Recruiting
Active, Not Recruiting
Not Yet Recruiting
Completed
Enrolling by Invitation

Showing 20 of 152 results

Not applicableEnded earlyNCT00896740
What this trial is testing

Gene Function in Bone Marrow Cells From Patients With Fanconi Anemia and From Healthy Participants

Who this might be right for
Fanconi Anemia
OHSU Knight Cancer Institute 90
Testing effectiveness (Phase 2)Study completedNCT00630253
What this trial is testing

Cytoxan, Fludara, and Antithymocyte Globulin Conditioning Followed By Stem Cell Transplant in Treating Fanconi Anemia

Who this might be right for
Fanconi Anemia
Masonic Cancer Center, University of Minnesota 31
Large-scale testing (Phase 3)Study completedNCT00176878
What this trial is testing

Stem Cell Transplant for Bone Marrow Failure Syndromes

Who this might be right for
Diamond-Blackfan AnemiaKostmann's NeutropeniaShwachman-Diamond Syndrome
Masonic Cancer Center, University of Minnesota 10
Testing effectiveness (Phase 2)Study completedNCT00919503
What this trial is testing

Treosulfan and Fludarabine Phosphate Before Donor Stem Cell Transplant in Treating Patients With Nonmalignant Inherited Disorders

Who this might be right for
Non-Neoplastic Hematologic and Lymphocytic Disorder
Fred Hutchinson Cancer Center 98
Testing effectiveness (Phase 2)Not Yet RecruitingNCT07408583
What this trial is testing

Prenatal Transplantation for Fetuses With Fanconi Anemia

Who this might be right for
Fanconi AnemiaAnemia, Hypoplastic, CongenitalCongenital Bone Marrow Failure Syndromes+5 more
Agnieszka Czechowicz 12
Testing effectiveness (Phase 2)Ended earlyNCT00167206
What this trial is testing

Stem Cell Transplantation for Fanconi Anemia

Who this might be right for
Fanconi Anemia
Masonic Cancer Center, University of Minnesota 16
Testing effectiveness (Phase 2)Study completedNCT00578435
What this trial is testing

Allogeneic Bone Marrow Transplantation for the Treatment of Genetic Disorders of Erythropoiesis

Who this might be right for
Genetic DisordersSickle Cell Anemia
Memorial Sloan Kettering Cancer Center 25
Early research (Phase 1)UnknownNCT00006127
What this trial is testing

Phase I Study of Amifostine in Patients With Bone Marrow Failure Related to Fanconi's Anemia

Who this might be right for
Fanconi's Anemia
Dana-Farber Cancer Institute 21
Testing effectiveness (Phase 2)UnknownNCT02386267
What this trial is testing

L-leucine in Diamond Blackfan Anemia Patients

Who this might be right for
Diamond Blackfan Anemia
Federal Scientific Clinical Centre of Pediatric Hematology, Oncology and Immunology named after Dmitry Rogache 30
Testing effectiveness (Phase 2)Study completedNCT01362595
What this trial is testing

Pilot Phase I/II Study of Amino Acid Leucine in Treatment of Patients With Transfusion-Dependent Diamond Blackfan Anemia

Who this might be right for
Diamond Blackfan AnemiaBlackfan Diamond SyndromeDBA+2 more
Northwell Health 55
Testing effectiveness (Phase 2)Active Not RecruitingNCT02061800
What this trial is testing

CD34+ (Malignant) Stem Cell Selection for Patients Receiving Allogenic Stem Cell Transplant

Who this might be right for
Chronic Myeloid Leukemia (CML)Acute Myelogenous Leukemia (AML)Myelodysplastic Syndrome (MDS)+3 more
Diane George 14
Testing effectiveness (Phase 2)Ended earlyNCT02065869
What this trial is testing

Safety Study of Gene Modified Donor T-cells Following TCRαβ+ Depleted Stem Cell Transplant

Who this might be right for
Acute Lymphoblastic LeukemiaLeukemia, Acute Myeloid (AML), ChildLymphoma, Non-Hodgkin+10 more
Bellicum Pharmaceuticals 187
Not applicableStudy completedNCT06490510
What this trial is testing

Prognostic Significance of Mutation Type and Chromosome Fragility in Fanconi Anemia

Who this might be right for
Fanconi Anemia
Fundació Institut de Recerca de l'Hospital de la Santa Creu i Sant Pau 227
Testing effectiveness (Phase 2)Ended earlyNCT04638517
What this trial is testing

The TELO-SCOPE Study: Attenuating Telomere Attrition With Danazol. Is There Scope to Dramatically Improve Health Outcomes for Adults and Children With Pulmonary Fibrosis

Who this might be right for
Pulmonary FibrosisTelomere ShorteningTelomere Disease+1 more
The University of Queensland 29
Not applicableEnrolling By InvitationNCT04437771
What this trial is testing

Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy

Who this might be right for
Fanconi Anemia Complementation Group AFanconi Anemia
Rocket Pharmaceuticals Inc. 9
Not applicableStudy completedNCT00005893
What this trial is testing

Study of Allogeneic Bone Marrow Transplantation Using Matched, Related Donors in Patients With Nonmalignant Hematologic Disorders

Who this might be right for
NeutropeniaSickle Cell AnemiaThalassemia Major+1 more
Fairview University Medical Center
Testing effectiveness (Phase 2)WithdrawnNCT04522375
What this trial is testing

A Dose Escalation Study of FP-045 in Patients With Fanconi Anemia

Who this might be right for
Fanconi Anemia
Foresee Pharmaceuticals Co., Ltd.
Not applicableLooking for participantsNCT06744283
What this trial is testing

Experience and Management of Cancer Screening-Related Anxiety in Fanconi Anemia

Who this might be right for
Fanconi Anemia
National Cancer Institute (NCI) 20
Testing effectiveness (Phase 2)Looking for participantsNCT06839456
What this trial is testing

Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT

Who this might be right for
LeukemiaHigh Risk Acute Lymphoblastic LeukemiaHigh Risk Acute Myeloid Leukemia+11 more
Children's Hospital of Philadelphia 100
Not applicableLooking for participantsNCT01758042
What this trial is testing

Bone Marrow and Kidney Transplant for Patients With Chronic Kidney Disease and Blood Disorders

Who this might be right for
Chronic Kidney DiseaseAcute Myeloid Leukemia (AML)Acute Lymphoblastic Leukemia (ALL)+14 more
Massachusetts General Hospital 10
Load More Results