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Results for “Inherited BMF Syndrome”

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Showing 20 of 0 results

Testing effectiveness (Phase 2)Active Not RecruitingNCT05796570
What this trial is testing

A Pilot Study to Evaluate the Feasibility of Post-Hematopoietic Stem Cell Transplant Prophylaxis With Decitabine Combined With Filgrastim for Children and Young Adults With AML, MDS and Related Myeloid Malignancies

Who this might be right for
Acute Myeloid LeukemiaMyelodysplastic SyndromesMyeloid Malignancies+4 more
Franziska Wachter 29
Not applicableStudy completedNCT00900055
What this trial is testing

Research Study in Healthy Volunteers of Patients With Fanconi Anemia, Myeloproliferative Disorders, or Myeloma

Who this might be right for
Chronic Myeloproliferative DisordersFanconi AnemiaMultiple Myeloma and Plasma Cell Neoplasm+1 more
OHSU Knight Cancer Institute 213
Large-scale testing (Phase 3)Study completedNCT00176852
What this trial is testing

Stem Cell Transplant for Hemoglobinopathy

Who this might be right for
Sickle Cell DiseaseThalassemiaSevere Congenital Neutropenia+2 more
Masonic Cancer Center, University of Minnesota 22
Testing effectiveness (Phase 2)Study completedNCT05828108
What this trial is testing

Study of the Selective GlyT1 Inhibitor Bitopertin for Steroid-Refractory Diamond-Blackfan Anemia

Who this might be right for
Steroid-refractory Diamond-Blackfan Anemia (DBA)
National Heart, Lung, and Blood Institute (NHLBI) 15
Early research (Phase 1)Ended earlyNCT02231710
What this trial is testing

Safety Study of Gene Modified Donor T Cell Infusion After Stem Cell Transplant for Non-Malignant Diseases

Who this might be right for
Primary Immune Deficiency DisordersHemophagocytic LymphohistiocytosisInherited Bone Marrow Failure Syndrome+2 more
Bellicum Pharmaceuticals 1
Not applicableStudy completedNCT03609840
What this trial is testing

Study of Thiotepa and TEPA Drug Exposure in Pediatric Hematopoietic Stem Cell Transplant Patients

Who this might be right for
Hematologic MalignanciesNonmalignant DiseasesImmune Deficiency+5 more
University of California, San Francisco 25
Not applicableStudy completedNCT00005892
What this trial is testing

Study of Allogeneic Bone Marrow Transplantation Following Cyclophosphamide and Radiotherapy in Patients With Myelodysplastic Syndrome and Acute Leukemia Related to Fanconi's Anemia

Who this might be right for
Fanconi's AnemiaMyelodysplastic SyndromesLeukemia, Nonlymphocytic, Acute+1 more
Fairview University Medical Center
Testing effectiveness (Phase 2)Ended earlyNCT01464164
What this trial is testing

Safety and Efficacy Study of Sotatercept in Adults With Transfusion Dependent Diamond Blackfan Anemia

Who this might be right for
Diamond Blackfan Anemia
Northwell Health 19
Testing effectiveness (Phase 2)Study completedNCT03513328
What this trial is testing

Conditioning Regimen for Allogeneic Hematopoietic Stem-Cell Transplantation

Who this might be right for
Bone Marrow Failure SyndromeThalassemiaSickle Cell Disease+13 more
University of Florida 6
Not applicableStudy completedNCT06490510
What this trial is testing

Prognostic Significance of Mutation Type and Chromosome Fragility in Fanconi Anemia

Who this might be right for
Fanconi Anemia
Fundació Institut de Recerca de l'Hospital de la Santa Creu i Sant Pau 227
Not applicableLooking for participantsNCT07186179
What this trial is testing

Mobilization of CD34+ Peripheral Blood Stem Cells in Patients With Diamond Blackfan Anemia Syndrome (DBAS)

Who this might be right for
Diamond Blackfan Anemia
Northwell Health 10
Not applicableAvailableNCT01995305
What this trial is testing

Use Massive Parallel Sequencing and Exome Capture Technology to Sequence the Exome of Fanconi Anemia Children and Their Patents

Who this might be right for
Fanconi AnemiaAutosomal or Sex Linked Recessive Genetic DiseaseBone Marrow Hematopoiesis Failure, Multiple Congenital Abnormalities, and Susceptibility to Neoplastic Diseases.+1 more
Xiaofan Zhu
Testing effectiveness (Phase 2)Looking for participantsNCT04099966
What this trial is testing

AlloSCT for Malignant and Non-malignant Hematologic Diseases Utilizing Alpha/Beta T Cell and CD19+ B Cell Depletion

Who this might be right for
Acute LeukemiaSevere Aplastic AnemiaNon-hodgkin Lymphoma+6 more
Mitchell Cairo 20
Testing effectiveness (Phase 2)Ended earlyNCT02065869
What this trial is testing

Safety Study of Gene Modified Donor T-cells Following TCRαβ+ Depleted Stem Cell Transplant

Who this might be right for
Acute Lymphoblastic LeukemiaLeukemia, Acute Myeloid (AML), ChildLymphoma, Non-Hodgkin+10 more
Bellicum Pharmaceuticals 187
Not applicableStudy completedNCT01316549
What this trial is testing

Study of Fludarabine Drug Exposure in Pediatric Bone Marrow Transplantation

Who this might be right for
Hematologic MalignanciesNonmalignant DiseasesImmunodeficiencies+5 more
University of California, San Francisco 67
Testing effectiveness (Phase 2)Study completedNCT00001749
What this trial is testing

Medical Treatment for Diamond Blackfan Anemia

Who this might be right for
Fanconi's AnemiaHematologic Disease
National Heart, Lung, and Blood Institute (NHLBI) 25
Testing effectiveness (Phase 2)Study completedNCT00004787
What this trial is testing

Phase II Pilot Study of Granulocyte Colony-Stimulating Factor for Inherited Bone Marrow Failure Syndromes

Who this might be right for
Shwachman SyndromeFanconi's AnemiaDyskeratosis Congenita+1 more
National Center for Research Resources (NCRR) 20
Not applicableLooking for participantsNCT05012111
What this trial is testing

Natural History of Acquired and Inherited Bone Marrow Failure Syndromes

Who this might be right for
Severe Aplastic AnemiaTelomere Biology DisordersInherited Bone Marrow Failure Syndromes
National Heart, Lung, and Blood Institute (NHLBI) 1,000
Testing effectiveness (Phase 2)Study completedNCT02931071
What this trial is testing

Clinical Phase II Trial to Evaluate CD34+ Cells Mobilization and Collection in Patients With Fanconi Anemia for Subsequent Transduction With a Lentiviral Vector Carring FANCA Gene. FANCOSTEM-1

Who this might be right for
Fanconi Anemia
Hospital Universitari Vall d'Hebron Research Institute 13
Testing effectiveness (Phase 2)Study completedNCT02797977
What this trial is testing

A Phase 1/2 Trial SRA737 in Combination With Gemcitabine and Cisplatin or Gemcitabine Alone in Advanced Cancer Subjects

Who this might be right for
Advanced Solid Tumors
Sierra Oncology LLC - a GSK company 153
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