Very early researchStudy completedNCT01339494What this trial is testingNitric Oxide Production in MELAS SyndromeWho this might be right forMELAS Syndrome Baylor College of Medicine 30
Early research (Phase 1)Study completedNCT02544217What this trial is testingA Dose-escalating Clinical Trial With KH176Who this might be right forMELASLHONLeigh Syndrome+2 more Khondrion BV 32
Early research (Phase 1)Study completedNCT03952234What this trial is testingL-Citrulline Dose Finding Safety Study in MELASWho this might be right forMELAS Syndrome Baylor College of Medicine 10
Testing effectiveness (Phase 2)Temporarily pausedNCT04846036What this trial is testingThe KHENERGYC StudyWho this might be right forMitochondrial DiseasesMitochondrial DNA tRNALeu(UUR) m.3243A<G MutationMELAS+1 more Khondrion BV 24
Large-scale testing (Phase 3)Ended earlyNCT04378075What this trial is testingEvaluate Efficacy and Safety of Vatiquinone for Treating Mitochondrial Disease in Participants With Refractory EpilepsyWho this might be right forMitochondrial DiseasesDrug Resistant EpilepsyLeigh Disease+5 more PTC Therapeutics 68
Large-scale testing (Phase 3)Looking for participantsNCT05541276What this trial is testingMELAtonin for Prevention of Postoperative Agitation and Emergence Delirium in ChildrenWho this might be right forEmergence Delirium Arash Afshari 676
Not applicableLooking for participantsNCT01694940What this trial is testingNorth American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)Who this might be right forMitochondrial DisordersMitochondrial Genetic DisordersMitochondrial Diseases+2 more Columbia University 1,000
Testing effectiveness (Phase 2)Study completedNCT06644534What this trial is testingAssess TTI-0102 vs Placebo in MELAS PatientsWho this might be right forMELAS SyndromeMitochondrial Encephalomyopathy, Lactic Acidosis and Stroke-like Episodes (MELAS) Thiogenesis Therapeutics, Inc. 9
Early research (Phase 1)Study completedNCT02570581What this trial is testingMELA Study - Hedonic Study on the Taste of Drugs Crushed in Food: Observational Study Involving 16 Healthy VolunteersWho this might be right forHealthy Centre Hospitalier Universitaire de Nice 16
Testing effectiveness (Phase 2)Active Not RecruitingNCT06961344What this trial is testingAn Open-label Extension Safety Study of MELAS Patients Who Completed TIS6463-203 (PRIZM)Who this might be right forMitochondrial Encephalopathy, Lactic Acidosis and Stroke-Like Episodes (MELAS Syndrome) Tisento Therapeutics 44
Not applicableNot Yet RecruitingNCT06013397What this trial is testingEffectiveness of Ketogenic Diet in MELAS SyndromeWho this might be right forMELAS SyndromeKetogenic Dieting Second Affiliated Hospital, Zhejiang University, School of Medicine 100
Not applicableLooking for participantsNCT01532791What this trial is testingNatural History Study - Mitochondrial DiseaseWho this might be right forMELAS or m.3243 A>G Mitochondrial DNA Mutation Carrier Columbia University 300
Very early researchStudy completedNCT01252979What this trial is testingKetones & Mitochondrial HeteroplasmyWho this might be right forMELAS SyndromeMitochondrial Diseases The University of Texas Health Science Center, Houston 13
Not applicableStudy completedNCT04948138What this trial is testingGlutamine Supplement in MELAS (Mitochondrial Encephalopathy, Lactic Acidosis, and Stroke-like Episodes) SyndromeWho this might be right forMELAS Syndrome Jesús González de la Aleja Tejera 9
Not applicableEnrolling By InvitationNCT01803906What this trial is testingTissue Sample Study for Mitochondrial DisordersWho this might be right forMitochondrial DisordersMitochondrial DiseaseMelas+6 more Columbia University 6,900
Early research (Phase 1)Looking for participantsNCT05241262What this trial is testingStudy of N-acetylcysteine in the Treatment of Patients With the m.3243A>G Mutation and Low Brain Glutathione LevelsWho this might be right forMitochondrial Disease Michio Hirano, MD 18
Not applicableStudy completedNCT00004353What this trial is testingStudy of the Metabolism of Pyruvate and Related Problems in Patients With Lactic AcidemiaWho this might be right forMitochondrial MyopathyMELAS SyndromeLactic Acidosis National Center for Research Resources (NCRR) 35
Large-scale testing (Phase 3)Looking for participantsNCT06451757What this trial is testingKHENERFIN Study: A Trial to Evaluate the Efficacy and Safety of Sonlicromanol in Primary Mitochondrial DiseasesWho this might be right forMitochondrial DiseasesMaternally Inherited Diabetes and Deafness (MIDD)Mitochondrial Encephalomyopathy, Lactic Acidosis and Stroke-like Episodes (MELAS)+1 more Khondrion BV 220
Testing effectiveness (Phase 2)Study completedNCT04604548What this trial is testingThe KHENEREXT StudyWho this might be right forMitochondrial DiseasesMitochondrial DNA tRNALeu(UUR) m.3243A<G MutationMaternally Inherited Diabetes and Deafness (MIDD)+2 more Khondrion BV 11
Not applicableStudy completedNCT06180421What this trial is testingMitochondrial Video Assessment Source Material StudyWho this might be right forPolG, Primary Mitochondrial Myopathy The Emmes Company, LLC 28