Large-scale testing (Phase 3)Study completedNCT01966029What this trial is testingBMN 110 Phase 3B in Australian PatientsWho this might be right forMucopolysaccharidosis IVA (Morquio A Syndrome) BioMarin Pharmaceutical 13
Not applicableStudy completedNCT04203290What this trial is testingEnd Tidal Anesthetic Concentration in Different Anesthesia Techniques Where Depth of Anesthesia Adjusted With EntropyWho this might be right forGeneral AnesthesiaInhalation; Gas Istanbul University 44
Not applicableStudy completedNCT01961518What this trial is testingScreening an Orthopedic Population for Mildly-affected Individuals With Morquio Syndrome A and Maroteaux-Lamy SyndromeWho this might be right forMorquio Syndrome AMaroteaux Lamy SyndromeMPS IVA+1 more Greenwood Genetic Center 17
Not applicableStudy completedNCT01870375What this trial is testingLongitudinal Studies of Brain Structure and Function in MPS DisordersWho this might be right forMucopolysaccharidosis Type IMucopolysaccharidosis Type IIMucopolysaccharidosis Type VI+2 more University of Minnesota 100
Testing effectiveness (Phase 2)Ended earlyNCT06067425What this trial is testingSafety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of SAR442501 in Pediatric Participants With AchondroplasiaWho this might be right forOsteochondrodysplasia Sanofi 16
Post-approval studies (Phase 4)Ended earlyNCT00609440What this trial is testingMorquio's Syndrome: a Case StudyWho this might be right forMorquio's Disease Clínica de Hidroterapia e Recuperacao Funcional 1
Post-approval studies (Phase 4)Looking for participantsNCT04152551What this trial is testingEffects of Bisphosphonates on OI-Related Hearing LossWho this might be right forOsteogenesis Imperfecta Hospital for Special Surgery, New York 100
Not applicableLooking for participantsNCT05408715What this trial is testingA Natural History Study in Children With a Type II Collagen Disorder With Short StatureWho this might be right forSEDCHypochondrogenesisSemd, Strudwick Type+1 more Innoskel 60
Not applicableStudy completedNCT05242913What this trial is testingEffects of Resistant Potato Starch on the Gut MicrobiotaWho this might be right forMicrobiota MSP Starch Products Inc. 75
Post-approval studies (Phase 4)Study completedNCT05058391What this trial is testingElaprase in Children and Adults With Hunter Syndrome (Mucopolysaccharidosis II) in IndiaWho this might be right forHunter Syndrome Takeda 5
Not applicableLooking for participantsNCT05284006What this trial is testingNon-invasive Functional Assessment and Pathogenesis of Morquio AWho this might be right forMucopolysaccharidosis IV Type AMorquio A SyndromeMPS IVA Nemours Children's Clinic 60
Not applicableEnded earlyNCT00787995What this trial is testingA Clinical Assessment Study of Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)Who this might be right forMPS IV AMucopolysaccharidosis IVAMorquio A Syndrome BioMarin Pharmaceutical 353
Not applicableUnknownNCT05283707What this trial is testingThe Effect of Paula Method Exercises on Post-cesarean Section DistensionWho this might be right forCesarean Section Complications Akdeniz University 80
Not applicableStudy completedNCT01920828What this trial is testingGait Analysis in MPS IVAWho this might be right forMPS IVAMorquio Syndrome Oregon Health and Science University 10
Testing effectiveness (Phase 2)Study completedNCT01515956What this trial is testingStudy of BMN 110 in Pediatric Patients < 5 Years of Age With Mucopolysaccharidosis IVA (Morquio A Syndrome)Who this might be right forMucopolysaccharidosis IVAMorquio A SyndromeMPS IVA BioMarin Pharmaceutical 15
Not applicableStudy completedNCT03971227What this trial is testingClinical Evaluation of Acuity 200 (Fluoroxyfocon A) RGP Contact LensWho this might be right forRefractive Errors Acuity Polymers, Inc. 74
Not applicableStudy completedNCT01475474What this trial is testingEvaluate the Safety, Tolerability and Effectiveness of the Renew Insert in Treating Accidental Bowel LeakageWho this might be right forBowel Incontinence Renew Medical 97
Not applicableEnrolling By InvitationNCT05368038What this trial is testingScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening ProgramWho this might be right forAcid Sphingomyelinase DeficiencyCeroid Lipofuscinosis, Neuronal, 2Cerebrotendinous Xanthomatosis+11 more Albert Einstein College of Medicine 100,000
Not applicableStudy completedNCT02067650What this trial is testingUltrasound Findings of Finger, Wrist and Knee Joints in MucopolysaccharidosisWho this might be right forMPS IMPS IV Children's Hospital of Eastern Ontario 18
Testing effectiveness (Phase 2)Active Not RecruitingNCT05845749What this trial is testingSafety and Efficacy of Voxzogo for Growth Deficits in MPS IVA and VIWho this might be right forMPS IVAMPS VI University of California, San Francisco 6