Large-scale testing (Phase 3)Study completedNCT01421992What this trial is testingMethylphenidate in Myotonic Dystrophy Type 1Who this might be right forDystrophia Myotonica 1 Laval University 28
Testing effectiveness (Phase 2)Looking for participantsNCT06844214What this trial is testingInvestigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1Who this might be right forMyotonic Dystrophy Sanofi 32
Large-scale testing (Phase 3)WithdrawnNCT04700046What this trial is testingStudy to Investigate the Efficacy and Safety of Mexiletine in Patients With Myotonic Dystrophy Type 1 and Type 2Who this might be right forMyotonic Dystrophy Type 1 and Type 2 Lupin Ltd.
Testing effectiveness (Phase 2)Active Not RecruitingNCT06185764What this trial is testingVX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1)Who this might be right forMyotonic Dystrophy Type 1 (DM1) Vertex Pharmaceuticals Incorporated 47
Early research (Phase 1)Study completedNCT00346255What this trial is testingBB-10901 in Treating Patients With Relapsed and/or Refractory Multiple MyelomaWho this might be right forMultiple Myeloma ImmunoGen, Inc. 37
Not applicableStudy completedNCT04907162What this trial is testingMusculoskeletal Nociceptive Pain in Participants With Neuromuscular DisordersWho this might be right forPompe Disease (Late-onset)Myotonic Dystrophy Type 1 (DM1)Myotonic Dystrophy Type 2+4 more LMU Klinikum 82
Testing effectiveness (Phase 2)Study completedNCT05027269What this trial is testingStudy of AOC 1001 in Adult Myotonic Dystrophy Type 1 (DM1) PatientsWho this might be right forDM1Myotonic Dystrophy 1Myotonic Dystrophy+5 more Avidity Biosciences, Inc. 39
Testing effectiveness (Phase 2)Looking for participantsNCT06667453What this trial is testingA Clinical Study of PGN-EDODM1 in People With Myotonic Dystrophy Type 1Who this might be right forMyotonic Dystrophy 1 PepGen Inc 24
Not applicableLooking for participantsNCT07136844What this trial is testingGait Analysis Parameter and Upper Limb Evaluation in Adult Patients With Neurological or Metabolic PathologyWho this might be right forNeuromuscular DiseasesObesity (Disorder)Myotonic Dystrophy 1+9 more Centre Hospitalier Universitaire de Liege 300
Not applicableLooking for participantsNCT00082108What this trial is testingMyotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy RegistryWho this might be right forMyotonic DystrophyFacioscapulohumeral Muscular DystrophyMuscular Dystrophy+6 more University of Rochester 3,000
Large-scale testing (Phase 3)Enrolling By InvitationNCT06549400What this trial is testingAn Open-Label Extension Study to Evaluate the Long-Term Safety and Efficacy of Once Daily Mexiletine PR in Patients With Myotonic Dystrophy Type 1 and Type 2 Who Have Completed MEX-DM-302 Study.Who this might be right forMyotonic Dystrophy Lupin Ltd. 176
Not applicableLooking for participantsNCT06708468What this trial is testingPersonalized Training for People With Rare Neuromuscular DisordersWho this might be right forNeuromuscular Diseases (NMD)Charcot Marie Tooth Disease (CMT)Facioscapulohumeral Muscular Dystrophy+1 more Oslo University Hospital 120
Not applicableStudy completedNCT03087526What this trial is testingNIPD on CFTC for Triplet Repeat DiseasesWho this might be right forNon Invasive Prenatal Diagnosis University Hospital, Montpellier 60
Very early researchLooking for participantsNCT06828588What this trial is testingPilot Study of [68Ga]Ga-ABY-025 Imaging in Patients Undergoing Treatment With HER2-targeted TherapyWho this might be right forLocally Advanced CancerMetastatic CancerHER2+2 more Vanderbilt-Ingram Cancer Center 30
Not applicableEnrolling By InvitationNCT07072676What this trial is testingThe Use of Assistive Gait Devices Can Reduce the Risk of Falls in Patients With Neuromuscular Diseases Following a Training Period.Who this might be right forInclusion Body MyositisMyotonic Dystrophy 1Myotonic Dystrophy 2+10 more LMU Klinikum 30
Testing effectiveness (Phase 2)Study completedNCT05479981What this trial is testingExtension of AOC 1001-CS1 (MARINA) Study in Adult Myotonic Dystrophy Type 1 (DM1) PatientsWho this might be right forDM1Muscular DystrophiesMyotonic Dystrophy+10 more Avidity Biosciences, Inc. 37
Large-scale testing (Phase 3)Looking for participantsNCT06523400What this trial is testingThe Efficacy and Safety of Once Daily Mexiletine PR in Patients With Myotonic Dystrophy Type 1 and Type 2Who this might be right forMyotonic Dystrophy Lupin Ltd. 176
Not applicableLooking for participantsNCT04003363What this trial is testingThe United Kingdom National Registry for Myotonic DystrophyWho this might be right forMyotonic Dystrophy Newcastle University 900
Not applicableUnknownNCT03155594What this trial is testingCGM to Aid Transition From Inpatient to OutpatientWho this might be right forDiabete Mellitus Methodist Medical Center of Illinois 15
Not applicableEnrolling By InvitationNCT05854433What this trial is testingBrain Structure and Clinical Endpoints in Myotonic Dystrophy Type 2Who this might be right forMyotonic Dystrophy Type 2Myotonic Dystrophy Type 1 Wake Forest University Health Sciences 100