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Results for “RARE DISEASE”

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Showing 20 of 0 results

Not applicableStudy completedNCT03290469
What this trial is testing

NICUSeq: A Trial to Evaluate the Clinical Utility of Human Whole Genome Sequencing (WGS) Compared to Standard of Care in Acute Care Neonates and Infants

Who this might be right for
Rare Diseases
Illumina, Inc. 355
Testing effectiveness (Phase 2)Study completedNCT00004670
What this trial is testing

Phase II Study of Pallidotomy for Parkinson Disease

Who this might be right for
Parkinson Disease
National Center for Research Resources (NCRR) 60
Not applicableStudy completedNCT00955370
What this trial is testing

The Experience of Uncertainty in Parents of Children With an Undiagnosed Medical Condition

Who this might be right for
Multiple Abnormalities
National Human Genome Research Institute (NHGRI) 500
Not applicableUnknownNCT03683966
What this trial is testing

MigALastat Therapy Adherence Among FABRY Patients: A Prospective Multicentral Observational Study

Who this might be right for
Rare DiseasesFabry DiseaseAdherence, Medication+1 more
Wuerzburg University Hospital 30
Not applicableStudy completedNCT00004805
What this trial is testing

Study of the Effect of Four Methods of Cardiopulmonary Resuscitation Instruction on Psychosocial Response of Parents With Infants at Risk of Sudden Death

Who this might be right for
Pulmonary HypertensionBronchopulmonary DysplasiaRespiratory Distress Syndrome
National Center for Research Resources (NCRR) 500
Testing effectiveness (Phase 2)Ended earlyNCT05537766
What this trial is testing

Study of Brexucabtagene Autoleucel in Adults With Rare B-cell Malignancies

Who this might be right for
Relapsed/Refractory Waldenstrom MacroglobulinemiaRelapsed/Refractory Richter TransformationRelapsed/Refractory Burkitt Lymphoma+1 more
Kite, A Gilead Company 19
Early research (Phase 1)Study completedNCT00004496
What this trial is testing

Phase I Study of Alpha-Melanocyte Stimulating Hormone in Patients With Acute Renal Failure

Who this might be right for
Acute Renal Failure
University of Texas 45
Not applicableEnded earlyNCT00004442
What this trial is testing

Study of Bile Acids in Patients With Peroxisomal Disorders

Who this might be right for
Infantile Refsum's DiseaseZellweger SyndromeBifunctional Enzyme Deficiency+1 more
University of Cincinnati 25
Not applicableStudy completedNCT00004696
What this trial is testing

Study of Morphine in Postoperative Infants to Allow Normal Ventilation

Who this might be right for
Infant, Newborn, DiseasesPain
Seattle Children's Hospital 100
Not applicableStudy completedNCT00004788
What this trial is testing

Study of Nutritional Factors in Porphyria

Who this might be right for
Porphyria
National Center for Research Resources (NCRR) 30
Not applicableStudy completedNCT00004838
What this trial is testing

Randomized Study of Succimer (Dimercaptosuccinic Acid) on Growth of Lead-Poisoned Children

Who this might be right for
Lead Poisoning
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) 175
Large-scale testing (Phase 3)Study completedNCT00006135
What this trial is testing

Phase III Randomized Study of Oral Acyclovir in Infants With Herpes Simplex Virus Infection Limited to Skin, Eyes, and Mouth

Who this might be right for
Herpes Simplex
National Center for Research Resources (NCRR) 66
Not applicableLooking for participantsNCT06795152
What this trial is testing

Rare Glycogen Storage Diseases Natural History Study

Who this might be right for
Glycogen Storage DiseaseGSD Type 0AGSD Type 0B+12 more
Duke University 200
Testing effectiveness (Phase 2)Active Not RecruitingNCT02978625
What this trial is testing

Talimogene Laherparepvec and Nivolumab in Treating Patients With Refractory Lymphomas or Advanced or Refractory Non-melanoma Skin Cancers

Who this might be right for
Anaplastic Large Cell Lymphoma, ALK-NegativeAnaplastic Large Cell Lymphoma, ALK-PositiveApocrine Carcinoma+36 more
National Cancer Institute (NCI) 68
Not applicableLooking for participantsNCT07575347
What this trial is testing

Periodontal Disease in Rare Renal Disorders (PERIO-RA-RE)

Who this might be right for
Periodontal DiseasePeriodontitisCKD+6 more
Stefan Lujinschi 100
Large-scale testing (Phase 3)Ended earlyNCT00450333
What this trial is testing

Dynepo Infrequent Dosing Study

Who this might be right for
AnemiaKidney Failure
Shire 407
Large-scale testing (Phase 3)Not Yet RecruitingNCT07786922
What this trial is testing

Avatrombopag in Adults With Aplastic Anemia Who Did Not Respond to, Cannot Receive, or Had Return of Disease After Standard Treatment

Who this might be right for
Aplastic Anemia
Swedish Orphan Biovitrum 26
Testing effectiveness (Phase 2)Study completedNCT02056665
What this trial is testing

Study to Evaluate the Efficacy and Safety of Minocycline in Angelman Syndrome

Who this might be right for
Angelman Syndrome
Puerta de Hierro University Hospital 32
Testing effectiveness (Phase 2)Looking for participantsNCT07823036
What this trial is testing

Assessing Pulmonary Changes in HSCT

Who this might be right for
HSCTRespiratoryGas Exchange Impairment
Children's Hospital Medical Center, Cincinnati 550
Not applicableStudy completedNCT00006130
What this trial is testing

Decompression Coring Versus Conservative Therapy in Patients With Avascular Necrosis of the Hip Related to Sickle Cell Disease

Who this might be right for
Bone Avascular NecrosisSickle Cell Anemia
UCSF Benioff Children's Hospital Oakland 50
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