Early research (Phase 1)Ended earlyNCT06681766What this trial is testingAssess Nomlabofusp in Adolescents and Children With Friedreich's AtaxiaWho this might be right forFriedreich Ataxia Larimar Therapeutics, Inc. 18
Very early researchStudy completedNCT02424435What this trial is testingMethylprednisolone Treatment of Friedreich AtaxiaWho this might be right forFriedreich Ataxia Children's Hospital of Philadelphia 11
Testing effectiveness (Phase 2)Study completedNCT07820579What this trial is testingSirolimus Treatment in Pediatric Patients With Ataxia-TelangiectasiaWho this might be right forAtaxia-Telangiectasia (A-T)Ataxia-Telangiectasia Sara Elva Espinosa Padilla, MD 6
Not applicableWithdrawnNCT06560346What this trial is testingUnderstanding the Natural History Early in the Course or Presentation of Friedreich AtaxiaWho this might be right forFriedreich AtaxiaRare Diseases Friedreich's Ataxia Research Alliance
Not applicableLooking for participantsNCT02497534What this trial is testingBiomarkers in Friedreich's AtaxiaWho this might be right forFriedreich's Ataxia University of Florida 203
Large-scale testing (Phase 3)Study completedNCT00656409What this trial is testingConjugate Pneumococcal Vaccine in Ataxia Telangiectasia (AT)Who this might be right forAtaxia Telangiectasia (AT) Institute of Child Health 30
Large-scale testing (Phase 3)Study completedNCT06193200What this trial is testingEvaluate the Neurological Effects of EryDex on Subjects With A-TWho this might be right forAtaxia Telangiectasia Quince Therapeutics S.p.A. 105
Early research (Phase 1)Study completedNCT04519567What this trial is testingMultiple Ascending Dose Study of CTI-1601 Versus Placebo in Subjects With Friedreich's AtaxiaWho this might be right forFriedreich Ataxia Larimar Therapeutics, Inc. 27
Not applicableWithdrawnNCT03770377What this trial is testingLaryngeal Adaptation for Speech and SwallowingWho this might be right forStrokeSpinocerebellar AtaxiaCerebral Stroke+2 more University of Florida
Testing effectiveness (Phase 2)WithdrawnNCT03182894What this trial is testingEpacadostat in Combination With Pembrolizumab and Azacitidine in Subjects With Metastatic Colorectal CancerWho this might be right forMetastatic Colorectal Cancer James J Lee
Not applicableEnded earlyNCT02246491What this trial is testingCell-Based Approaches For Modeling and Treating Ataxia-TelangiectasiaWho this might be right forAtaxia-Telangiectasia (A-T) Johns Hopkins University 6
Not applicableStudy completedNCT05028764What this trial is testingDetermine Range of Tissue Frataxin Concentrations and Other Potential BiomarkersWho this might be right forFriedreich AtaxiaHealthy Volunteers Larimar Therapeutics, Inc. 60
Early research (Phase 1)Looking for participantsNCT07180355What this trial is testingSGT-212 Gene Therapy in Friedreich's AtaxiaWho this might be right forFriedreich's Ataxia (FA) Solid Biosciences Inc. 10
Large-scale testing (Phase 3)Study completedNCT00697073What this trial is testingStudy to Assess the Safety and Tolerability of Idebenone in the Treatment of Friedreich's Ataxia PatientsWho this might be right forFriedreich's Ataxia Santhera Pharmaceuticals 68
Testing effectiveness (Phase 2)Study completedNCT00034242What this trial is testingHigh-Dose Intravenous Immunoglobulin to Treat Cerebellar DegenerationWho this might be right forSpinocerebellar Degenerations National Institute of Neurological Disorders and Stroke (NINDS) 20
Testing effectiveness (Phase 2)Looking for participantsNCT07506109What this trial is testingA Phase II Study of Sintilimab Combined With Ipilimumab N01, Cetuximab and Dabrafenib in Patients With Microsatellite-Stable, BRAF V600E-Mutated Metastatic Colorectal CancerWho this might be right forBRAF V600EColorectal CancerSintilimab+4 more Tianjin Medical University Cancer Institute and Hospital 49
Not applicableStudy completedNCT00187057What this trial is testingStudy for Treatment of Cancer in Children With Ataxia-telangiectasiaWho this might be right forAtaxia-Telangiectasia St. Jude Children's Research Hospital 6
Large-scale testing (Phase 3)Study completedNCT01970111What this trial is testingAn Extension Study of KPS-0373 in Patients With Spinocerebellar Degeneration (SCD)Who this might be right forSpinocerebellar Degeneration Kissei Pharmaceutical Co., Ltd.
Not applicableStudy completedNCT00136630What this trial is testingNatural History, Genetic Bases and Phenotype-genotype Correlations in Autosomal Dominant Spinocerebellar DegenerationsWho this might be right forSpinocerebellar AtaxiasSpastic Paraplegias Institut National de la Santé Et de la Recherche Médicale, France 175
Large-scale testing (Phase 3)Ended earlyNCT06664853What this trial is testingOpen-Label Extension of EryDex Study IEDAT-04-2022Who this might be right forAtaxia Telangiectasia Quince Therapeutics S.p.A. 101