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Results for “Transfusion Dependent Beta-Thalassemia”

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Showing 20 of 0 results

Large-scale testing (Phase 3)Study completedNCT01033747
What this trial is testing

Safety and Efficacy of Deferasirox in Patients With Transfusion Dependent Iron Overload - a Non-comparative Extension Study

Who this might be right for
Liver Iron Overload
Novartis Pharmaceuticals 70
Testing effectiveness (Phase 2)Study completedNCT03271541
What this trial is testing

Bitopertin (RO4917838) in Adults With Non-Transfusion-Dependent (NTD) Beta-Thalassemia

Who this might be right for
Beta-Thalassemia
Hoffmann-La Roche 12
Testing effectiveness (Phase 2)Study completedNCT07370922
What this trial is testing

Glucagon-Like Peptide 1 Receptor Agonist in Diabetes Mellitus Management in Children and Adolescents With Transfusion-Dependent Thalassemia

Who this might be right for
Transfusion Dependent Beta Thalassemia
Ain Shams University 80
Not applicableEnrolling By InvitationNCT06363760
What this trial is testing

A Long-Term Follow-Up Study of Participants With Sickle Cell Disease or Transfusion Dependent β-Thalassemia Who Received EDIT-301

Who this might be right for
Sickle Cell DiseaseTransfusion-dependent Beta-ThalassemiaHemoglobinopathies
Editas Medicine, Inc. 54
Not applicableActive Not RecruitingNCT05145062
What this trial is testing

Long - Term Follow Up of Sickle Cell Disease and Beta-thalassemia Subjects Previously Exposed to BIVV003 or ST-400.

Who this might be right for
Blood and Lymphatic Diseases
Sangamo Therapeutics 8
Testing effectiveness (Phase 2)Looking for participantsNCT05693909
What this trial is testing

A Trial Testing SP-420 in Subjects With Transfusion-dependent β-thalassemia or Low-risk Myelodysplastic Syndromes

Who this might be right for
Beta Thalassemia Major AnemiaMyelodysplastic Syndrome
Pharmacosmos A/S 90
Not applicableLooking for participantsNCT06219239
What this trial is testing

Safety and Efficacy of the Lentiviral Vector in Gene Therapy of Beta-thalassemia Patients

Who this might be right for
Transfusion-dependent Beta-Thalassemia
Institute of Hematology & Blood Diseases Hospital, China 3
Not applicableLooking for participantsNCT06298630
What this trial is testing

Long-term Follow-up Study of BRL-101 for TDT

Who this might be right for
Thalassemia, Beta
Bioray Laboratories 45
Large-scale testing (Phase 3)Active Not RecruitingNCT05356195
What this trial is testing

Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Transfusion-Dependent β-Thalassemia (TDT)

Who this might be right for
Beta-ThalassemiaThalassemiaGenetic Diseases, Inborn+2 more
Vertex Pharmaceuticals Incorporated 16
Very early researchNot Yet RecruitingNCT06678165
What this trial is testing

A Pilot Study on the Safety and Efficacy of YOLT-204 for Transfusion-Dependent Beta-Thalassemia

Who this might be right for
Transfusion Dependent Beta Thalassemia
First Affiliated Hospital of Guangxi Medical University 3
Testing effectiveness (Phase 2)Ended earlyNCT03381833
What this trial is testing

A Study With LJPC-401 for the Treatment of Myocardial Iron Overload in Patients With Transfusion-Dependent Beta Thalassemia

Who this might be right for
Beta-Thalassemia
La Jolla Pharmaceutical Company 84
Testing effectiveness (Phase 2)Study completedNCT03877809
What this trial is testing

Testing SIROLIMUS in Beta-thalassemia Transfusion Dependent Patients

Who this might be right for
Beta-Thalassemia
Rare Partners srl Impresa Sociale 26
Testing effectiveness (Phase 2)Study completedNCT03342404
What this trial is testing

Determine the Efficacy and Safety of Luspatercept in Adults With Non Transfusion Dependent Beta (β)-Thalassemia

Who this might be right for
Thalassemia
Celgene 145
Large-scale testing (Phase 3)Active Not RecruitingNCT04770753
What this trial is testing

A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Non-Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-NTDT)

Who this might be right for
Non-Transfusion-dependent Alpha-ThalassemiaNon-Transfusion-dependent Beta-Thalassemia
Agios Pharmaceuticals, Inc. 194
Large-scale testing (Phase 3)Study completedNCT03207009
What this trial is testing

A Study Evaluating the Efficacy and Safety of the LentiGlobin® BB305 Drug Product in Participants With Transfusion-Dependent β-Thalassemia

Who this might be right for
Beta-Thalassemia
Genetix Biotherapeutics Inc. 19
Not applicableStudy completedNCT02090699
What this trial is testing

MR Imaging of Diffuse Myocardial Fibrosis in Transfusion-Dependent Anemias

Who this might be right for
Thalassemia MajorChronic Blood Transfusion Related Iron Overload
University Health Network, Toronto 42
Not applicableNot Yet RecruitingNCT07480980
What this trial is testing

Evaluation of Micro RNA-155 Expression in Relation to Alloantibody Formation in Transfusion-Dependent Patients

Who this might be right for
Red Cell AlloantibodiesBlood Transfusion-DependentBeta Thalassemia
Assiut University 100
Large-scale testing (Phase 3)Active Not RecruitingNCT04770779
What this trial is testing

A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)

Who this might be right for
Transfusion-dependent Alpha-ThalassemiaTransfusion-dependent Beta-Thalassemia
Agios Pharmaceuticals, Inc. 258
Not applicableStudy completedNCT02626689
What this trial is testing

To Document the Burden of Illness on the Quality of Life and the Impact on Healthcare Utilization in (Beta) β-thalassemia Subjects Who Are Transfusion Dependent (TD) and Non-transfusion Dependent (NTD) Receiving Standard of Care

Who this might be right for
Beta-Thalassemia
Celgene 100
Large-scale testing (Phase 3)Looking for participantsNCT07517133
What this trial is testing

Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With α- or β-Non-Transfusion-Dependent Thalassemia

Who this might be right for
Non-Transfusion-dependent Alpha-ThalassemiaNon-Transfusion-dependent Beta-Thalassemia
Agios Pharmaceuticals, Inc. 45
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