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Results for “β-Thalassemia Major”

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Showing 20 of 0 results

Not applicableActive Not RecruitingNCT02633943
What this trial is testing

Long-term Follow-up of Subjects With Transfusion-Dependent β-Thalassemia (TDT) Treated With Ex Vivo Gene Therapy

Who this might be right for
Transfusion-dependent Beta-Thalassemia
Genetix Biotherapeutics Inc. 66
Testing effectiveness (Phase 2)Study completedNCT04364269
What this trial is testing

Safety, Tolerability, Pharmacokinetics (PK), Pharmacodynamics (PD) and Preliminary Efficacy of VIT-2763 in β-thalassaemia

Who this might be right for
Beta-ThalassemiaNon-transfusion-dependent Thalassemia
Vifor (International) Inc. 35
Post-approval studies (Phase 4)Study completedNCT03961828
What this trial is testing

Hyalornic Acid Level in β-Thalassemic Children Treated for Hepatitis C Virus

Who this might be right for
Beta-ThalassemiaHepatitis C
Tanta University 50
Large-scale testing (Phase 3)Study completedNCT03851055
What this trial is testing

Zinc Supplementation in Patients With β-Thalassemia Major Complicated With Diabetes Mellitus

Who this might be right for
Beta-thalassemia Major Complicated With Diabetes
Ain Shams University 80
Not applicableEnrolling By InvitationNCT06363760
What this trial is testing

A Long-Term Follow-Up Study of Participants With Sickle Cell Disease or Transfusion Dependent β-Thalassemia Who Received EDIT-301

Who this might be right for
Sickle Cell DiseaseTransfusion-dependent Beta-ThalassemiaHemoglobinopathies
Editas Medicine, Inc. 54
Not applicableUnknownNCT03847558
What this trial is testing

Sexual Maturation in β-Thalassemia Major Patients in Assiut University Hospital

Who this might be right for
β-Thalassemia Major Patients Receiving Chelation Therapy
Assiut University 100
Not applicableTemporarily pausedNCT05442346
What this trial is testing

Safety and Efficacy Evaluation of γ-globin Reactivated Autologous Hematopoietic Stem Cells

Who this might be right for
Thalassemia Major
Bioray Laboratories 5
Testing effectiveness (Phase 2)Looking for participantsNCT05693909
What this trial is testing

A Trial Testing SP-420 in Subjects With Transfusion-dependent β-thalassemia or Low-risk Myelodysplastic Syndromes

Who this might be right for
Beta Thalassemia Major AnemiaMyelodysplastic Syndrome
Pharmacosmos A/S 90
Not applicableLooking for participantsNCT06219239
What this trial is testing

Safety and Efficacy of the Lentiviral Vector in Gene Therapy of Beta-thalassemia Patients

Who this might be right for
Transfusion-dependent Beta-Thalassemia
Institute of Hematology & Blood Diseases Hospital, China 3
Not applicableLooking for participantsNCT06298630
What this trial is testing

Long-term Follow-up Study of BRL-101 for TDT

Who this might be right for
Thalassemia, Beta
Bioray Laboratories 45
Large-scale testing (Phase 3)Active Not RecruitingNCT05356195
What this trial is testing

Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Transfusion-Dependent β-Thalassemia (TDT)

Who this might be right for
Beta-ThalassemiaThalassemiaGenetic Diseases, Inborn+2 more
Vertex Pharmaceuticals Incorporated 16
Not applicableUnknownNCT02126046
What this trial is testing

Unrelated Umbilical Cord Blood Following HLA-haploidentical Hematopoietic Stem Cell Transplantation in Patients With β-thalassemia Major

Who this might be right for
Thalassemia Major
Nanfang Hospital, Southern Medical University 30
Testing effectiveness (Phase 2)Not Yet RecruitingNCT07489196
What this trial is testing

Safety and Efficacy Study Evaluating CS-101 in Participants With β-Thalassemia Major

Who this might be right for
β-thalassemia Major
CorrectSequence Therapeutics Co., Ltd 20
Testing effectiveness (Phase 2)Ended earlyNCT04205435
What this trial is testing

Β-globin Restored Autologous HSC in β-thalassemia Major Patients

Who this might be right for
β-thalassemia Major
Bioray Laboratories 2
Testing effectiveness (Phase 2)Study completedNCT03342404
What this trial is testing

Determine the Efficacy and Safety of Luspatercept in Adults With Non Transfusion Dependent Beta (β)-Thalassemia

Who this might be right for
Thalassemia
Celgene 145
Early research (Phase 1)Active Not RecruitingNCT01639690
What this trial is testing

SS-Thalassemia Major With Autologous CD34+ Hematopoietic Progenitor Cells Transduced With TNS9.3.55 a Lentiviral Vector Encoding the Normal Human ß-Globin Gene

Who this might be right for
Confirmed Diagnosis of ß-thalassemia Major
San Rocco Therapeutics 10
Testing effectiveness (Phase 2)UnknownNCT03014882
What this trial is testing

Sperm DNA Damage in β-thalassemia Major: Is There a Role for Antioxidants?

Who this might be right for
Endocrine DiseaseFertility Decreased MaleDNA Damage
Ain Shams University 30
Large-scale testing (Phase 3)Active Not RecruitingNCT04770753
What this trial is testing

A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Non-Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-NTDT)

Who this might be right for
Non-Transfusion-dependent Alpha-ThalassemiaNon-Transfusion-dependent Beta-Thalassemia
Agios Pharmaceuticals, Inc. 194
Large-scale testing (Phase 3)Study completedNCT03207009
What this trial is testing

A Study Evaluating the Efficacy and Safety of the LentiGlobin® BB305 Drug Product in Participants With Transfusion-Dependent β-Thalassemia

Who this might be right for
Beta-Thalassemia
Genetix Biotherapeutics Inc. 19
Not applicableLooking for participantsNCT06479616
What this trial is testing

A Long-term Follow-up Study in Participants Who Received CS-101

Who this might be right for
Beta-Thalassemia
Children's Hospital of Fudan University 5
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