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Results for “Mucopolysaccharidosis II”

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Showing 20 of 0 results

Not applicableStudy completedNCT01626092
What this trial is testing

Reduced-Intensity Hematopoietic Stem Cell Transplant for High Risk Lysosomal and Peroxisomal Disorders

Who this might be right for
Lysosomal Storage DiseasePeroxisomal Disorder
Masonic Cancer Center, University of Minnesota 3
Not applicableActive Not RecruitingNCT04597385
What this trial is testing

Long-term Follow-Up for RGX-121

Who this might be right for
Mucopolysaccharidosis II
REGENXBIO Inc. 27
Not applicableStudy completedNCT01521429
What this trial is testing

Longitudinal Study of Bone Disease in Children with Mucopolysaccharidoses (MPS) I, II, and VI

Who this might be right for
Mucopolysaccharidoses
Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center 55
Large-scale testing (Phase 3)Active Not RecruitingNCT07236606
What this trial is testing

RGX-121-3102 Gene Therapy in Participants With MPS II (Hunter Syndrome)

Who this might be right for
MPS IIHunter Syndrome (MPS II)
REGENXBIO Inc. 2
Testing effectiveness (Phase 2)Study completedNCT03411161
What this trial is testing

S 81694 Plus Paclitaxel in Metastatic Breast Cancer

Who this might be right for
Metastatic Breast CancerMetastatic Triple Negative Breast Cancer
Institut de Recherches Internationales Servier 22
Not applicableStudy completedNCT01822184
What this trial is testing

Observational Study to Evaluate Neurodevelopmental Status in Pediatric Patients With Hunter Syndrome (MPS II)

Who this might be right for
Mucopolysaccharidosis (MPS)Hunter Syndrome
Shire 100
Testing effectiveness (Phase 2)Study completedNCT03300453
What this trial is testing

Intracerebral Gene Therapy in Children With Sanfilippo Type B Syndrome

Who this might be right for
Sanfilippo Syndrome B
UniQure Biopharma B.V. 4
Testing effectiveness (Phase 2)Study completedNCT01506141
What this trial is testing

An Extension Study of HGT-HIT-045 Evaluating Long-Term Safety and Clinical Outcomes of Idursulfase-IT in Conjunction With Elaprase in Pediatric Participants With Hunter Syndrome and Cognitive Impairment

Who this might be right for
Hunter Syndrome
Takeda 15
Post-approval studies (Phase 4)Study completedNCT00607386
What this trial is testing

Safety and Clinical Outcomes in Hunter Syndrome Patients 5 Years of Age and Younger Receiving Idursulfase Therapy

Who this might be right for
Hunter SyndromeMucopolysaccharidosis IIMPS II
Shire 28
Not applicableStudy completedNCT01449240
What this trial is testing

Collection and Study of Cerebrospinal Fluid in Patients With Hunter Syndrome

Who this might be right for
Hunter Syndrome
Shire 10
Not applicableStudy completedNCT01602601
What this trial is testing

Test the Possibility of Cross Reaction Induced by the Idursulfase Drug to GSK2788723

Who this might be right for
Mucopolysaccharidosis II
GlaxoSmithKline 10
Testing effectiveness (Phase 2)Study completedNCT03513328
What this trial is testing

Conditioning Regimen for Allogeneic Hematopoietic Stem-Cell Transplantation

Who this might be right for
Bone Marrow Failure SyndromeThalassemiaSickle Cell Disease+13 more
University of Florida 6
Large-scale testing (Phase 3)Ended earlyNCT00654433
What this trial is testing

ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transfusion (UCBT) in Patients With Inherited Metabolic Diseases

Who this might be right for
Inherited Metabolic DiseasesLysosomal Storage DisordersPeroxisomal Storage Diseases+2 more
Aldagen 40
Testing effectiveness (Phase 2)Ended earlyNCT03041324
What this trial is testing

Ascending Dose Study of Genome Editing by the Zinc Finger Nuclease (ZFN) Therapeutic SB-913 in Subjects With MPS II

Who this might be right for
Mucopolysaccharidosis IIMPS II
Sangamo Therapeutics 9
Not applicableStudy completedNCT00001754
What this trial is testing

Study of Skeletal Disorders and Short Stature

Who this might be right for
Developmental Bone DiseaseDwarfismSkeletal Dysplasias
National Human Genome Research Institute (NHGRI) 600
Testing effectiveness (Phase 2)Study completedNCT00920647
What this trial is testing

A Safety and Dose Ranging Study of Idursulfase (Intrathecal) Administration Via an Intrathecal Drug Delivery Device in Pediatric Patients With Hunter Syndrome Who Have Central Nervous System Involvement and Are Receiving Treatment With Elaprase®

Who this might be right for
Hunter Syndrome
Shire 16
Post-approval studies (Phase 4)WithdrawnNCT05494593
What this trial is testing

ELAPRASE in Treatment-naïve Participants With Hunter Syndrome (Mucopolysaccharidosis [MPS] II)

Who this might be right for
Mucopolysaccharidosis (MPS)Hunter Syndrome
Takeda
Not applicableEnded earlyNCT01675674
What this trial is testing

Study to Detect Unrecognized Mucopolysaccharidosis in Children Visiting Rheumatology, Hand or Skeletal Dysplasia Clinics

Who this might be right for
MucopolysaccharidosesMucopolysaccharidosis IMucopolysaccharidosis II+2 more
National MPS Society 3,000
Testing effectiveness (Phase 2)UnknownNCT02663024
What this trial is testing

Study of Idursulfase-beta (GC1111) in Hunter Syndrome

Who this might be right for
Mucopolysaccharidosis II
Green Cross Corporation 20
Testing effectiveness (Phase 2)Active Not RecruitingNCT06095388
What this trial is testing

Phase I/II Study of JR-441 in Patients With Mucopolysaccharidosis Type IIIA

Who this might be right for
Mucopolysaccharidosis III-A
JCR Pharmaceuticals Co., Ltd. 15
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