Large-scale testing (Phase 3)Looking for participantsNCT04808505
What this trial is testing
Evaluate the Safety, Efficacy, PK, PD and Immunogenicity of Cipaglucosidase Alfa/Miglustat in IOPD Subjects Aged 0 to <18
Who this might be right for
Glycogen Storage Disease Type II Infantile Onset
Amicus Therapeutics 36