Testing effectiveness (Phase 2)UnknownNCT05588401What this trial is testingEvaluating Safety and Efficacy of Autologous Gene-edited Muscle Stem Cells (GenPHSats-bASKet)Who this might be right forLGMD Simone Spuler, MD 6
Testing effectiveness (Phase 2)Active Not RecruitingNCT05230459What this trial is testingEvaluate the Safety of AB-1003 (Previously LION-101) in Subjects With Genetic Confirmation of LGMD2I/R9 (Part1)Who this might be right forLimb Girdle Muscular DystrophyLimb-Girdle Muscular Dystrophy Type 2LGMD2I+6 more AskBio Inc 9
Not applicableStudy completedNCT02810028What this trial is testingAcceptance and Commitment Therapy for Muscle DiseaseWho this might be right forMuscle Diseases King's College Hospital NHS Trust 155
Early research (Phase 1)Study completedNCT00494195What this trial is testingGene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)Who this might be right forMuscular Dystrophies Nationwide Children's Hospital 6
Large-scale testing (Phase 3)Study completedNCT01035983What this trial is testingSafety and Tolerability of Frovatriptan to Prevention of Menstrually Associated Migraine (MAM) HeadachesWho this might be right forMigraine Endo USA Inc., a Keenova Therapeutics Company 550
Not applicableStudy completedNCT03127241What this trial is testingUser-centred Assistive System for Arm Functions in Neuromuscular SubjectsWho this might be right forMuscular DystrophiesMuscular Dystrophy, DuchenneMuscular Dystrophy, Becker+1 more Politecnico di Milano 38
Early research (Phase 1)Study completedNCT01344798What this trial is testingClinical Study of AAV1-gamma-sarcoglycan Gene Therapy for Limb Girdle Muscular Dystrophy Type 2CWho this might be right forLimb Girdle Muscular Dystrophy Type 2CGamma-sarcoglycanopathy Genethon 9
Not applicableStudy completedNCT01081080What this trial is testingCardiac Magnetic Resonance in Children With Muscular DystrophyWho this might be right forDuchenne Muscular DystrophyBecker Muscular DystrophyLimb Girdle Muscular Dystrophy Cooperative International Neuromuscular Research Group 20
Not applicableUnknownNCT01676077What this trial is testingClinical Outcome Study for DysferlinopathyWho this might be right forDysferlinopathyLGMD2B Now Classified as LGMDR2Miyoshi Myopathy Newcastle-upon-Tyne Hospitals NHS Trust 200
Testing effectiveness (Phase 2)Ended earlyNCT03652259What this trial is testingGene Delivery Clinical Trial of SRP-9003 (Bidridistrogene Xeboparvovec) for Participants With Limb-Girdle Muscular Dystrophy, Type 2E (LGMD2E) (Beta-Sarcoglycan Deficiency)Who this might be right forLimb-Girdle Muscular Dystrophy, Type 2E Sarepta Therapeutics, Inc. 6
Not applicableStudy completedNCT02428985What this trial is testingProspective, Non-interventional, Multi-center, Post-authorization Safety Study of Riociguat for Pulmonary Arterial Hypertension (PAH)Who this might be right forHypertension, Pulmonary Bayer 882
Testing effectiveness (Phase 2)Study completedNCT02841267What this trial is testingA Trial of PF-06252616 in Ambulatory Participants With LGMD2IWho this might be right forLGMD2I Kathryn Wagner 19
Large-scale testing (Phase 3)Active Not RecruitingNCT07678775What this trial is testingOpen-Label Extension Study of BBP-418 (Ribitol) for LGMD2I/R9Who this might be right forLimb-Girdle Muscular Dystrophy Type 2I (LGMD2I) ML Bio Solutions, Inc. 107
Not applicableStudy completedNCT00457912What this trial is testingGenetic Characterization of Individuals With Limb Girdle Muscular DystrophyWho this might be right forLimb-Girdle Muscular Dystrophy Nationwide Children's Hospital 277
Large-scale testing (Phase 3)Study completedNCT02285062What this trial is testingEfficacy and Safety Study of Lenalidomide Plus R-CHOP Chemotherapy Versus Placebo Plus R-CHOP Chemotherapy in Untreated ABC Type Diffuse Large B-cell LymphomaWho this might be right forLymphoma, Large B-Cell, Diffuse Celgene 570
Not applicableActive Not RecruitingNCT04475926What this trial is testingThe Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years of Age, Who Are Managed in Routine Clinical PracticeWho this might be right forLimb-girdle Muscular Dystrophy Sarepta Therapeutics, Inc. 205
Not applicableUnknownNCT03492346What this trial is testingLimb Girdle Muscular Dystrophy Type 2E Recruitment StudyWho this might be right forLimb-Girdle Muscular Dystrophy, Type 2E Nationwide Children's Hospital 25
Not applicableStudy completedNCT03842878What this trial is testingNatural History Study of Patients With Limb-Girdle Muscular Dystrophy 2IWho this might be right forLGMD2I Genethon 52
Not applicableActive Not RecruitingNCT05206617What this trial is testing3 Year Follow up on ANO5 PatientsWho this might be right forNeuromuscular DiseasesLimb Girdle Muscular Dystrophy Rigshospitalet, Denmark 17
Not applicableActive Not RecruitingNCT05102799What this trial is testingMRI-phenotyping of Patients With Pathogenic Anoctamin 5 VariantsWho this might be right forLimb Girdle Muscular Dystrophy Rigshospitalet, Denmark 200