Not applicableStudy completedNCT03626207What this trial is testingDevelopment of Visual Function Evaluation Method (2)Who this might be right forRetinitis Pigmentosa Astellas Pharma Inc 8
Not applicableEnrolling By InvitationNCT05921162What this trial is testingA Long-Term Follow-Up Study in Subjects Who Received vMCO-I Administered Via Intravitreal InjectionWho this might be right forRetinitis PigmentosaRetinal DiseaseRetinal Degeneration Nanoscope Therapeutics Inc. 11
Not applicableLooking for participantsNCT06092346What this trial is testingA Natural History Study Seeks to Understand the Clinical, Genomic, Pharmacological, Laboratory, and Dietary Determinates of Pyrimidine and Purine Metabolism DisordersWho this might be right forAMPD3, OMIM*102772, AMP Deaminase DeficiencyAK1, OMIM *103000, Adenylate Kinase DeficiencyAMPD1, OMIM *102770, Myopathy Due to Myoadenylate Deaminase Deficiency+25 more National Human Genome Research Institute (NHGRI)
Testing effectiveness (Phase 2)Looking for participantsNCT06627179What this trial is testingStudy to Evaluate Ultevursen in Subjects With Retinitis Pigmentosa (RP) Due to Mutations in Exon 13 of the USH2A GeneWho this might be right forRetinitis Pigmentosa (RP)Usher Syndrome Type 2Deaf Blind+4 more Laboratoires Thea 81
Not applicableLooking for participantsNCT06982417What this trial is testingInsightRP2 RegistryWho this might be right forRP2-associated Retinitis PigmentosaX-Linked Retinitis Pigmentosa (XLRP)Retinitis Pigmentosa 2 University of Göttingen 200
Testing effectiveness (Phase 2)Study completedNCT04604899What this trial is testingSafety of Repeat Intravitreal Injection of Human Retinal Progenitor Cells (jCell) in Adult Subjects With Retinitis PigmentosaWho this might be right forRetinitis Pigmentosa jCyte, Inc 30
Large-scale testing (Phase 3)Ended earlyNCT05158296What this trial is testingStudy to Evaluate the Efficacy Safety and Tolerability of Ultevursen in Subjects With RP Due to Mutations in Exon 13 of the USH2A Gene (Sirius)Who this might be right forRetinitis PigmentosaUsher Syndrome Type 2Deaf Blind+5 more Laboratoires Thea 7
Large-scale testing (Phase 3)Looking for participantsNCT06581406What this trial is testingA Randomized, Phase 2/3 Study to Investigate the Efficacy and Safety of RP2 in Combination With Nivolumab in Immune Checkpoint Inhibitor-Naïve Adult Patients With Metastatic Uveal MelanomaWho this might be right forMetastatic Uveal Melanoma Replimune, Inc. 280
Large-scale testing (Phase 3)Study completedNCT05194124What this trial is testingPhase 3 Crossover Trial of Two Formulations of Setmelanotide in Participants With Specific Gene Defects in the MC4R PathwayWho this might be right forBardet-Biedl SyndromePOMC Deficiency Rhythm Pharmaceuticals, Inc. 19
Testing effectiveness (Phase 2)Not Yet RecruitingNCT06952842What this trial is testingSafety and Efficacy of ZVS203e in the Treatment of Retinitis Pigmentosa Caused by RHO Gene MutationWho this might be right forRetinitis Pigmentosa Chigenovo Co., Ltd 18
Large-scale testing (Phase 3)Ended earlyNCT05176717What this trial is testingStudy to Evaluate the Efficacy Safety and Tolerability of QR-421a in Subjects With RP Due to Mutations in Exon 13 of the USH2A Gene With Early to Moderate Vision Loss (Celeste)Who this might be right forRetinitis PigmentosaUsher Syndrome Type 2Deaf Blind+5 more Laboratoires Thea 5
Testing effectiveness (Phase 2)Active Not RecruitingNCT06646289What this trial is testingA Follow-on Study for Second-Eye Treatment for Participants Previously Treated With Gene Therapy for X-Linked Retinitis Pigmentosa (XLRP)Who this might be right forX-Linked Retinitis Pigmentosa Janssen Research & Development, LLC 24
Testing effectiveness (Phase 2)Study completedNCT03780257What this trial is testingStudy to Evaluate Safety and Tolerability of QR-421a in Subjects With RP Due to Mutations in Exon 13 of the USH2A GeneWho this might be right forRetinitis PigmentosaUsher Syndrome Type 2Deaf Blind+5 more ProQR Therapeutics 20
Testing effectiveness (Phase 2)Ended earlyNCT05085964What this trial is testingAn Open-Label Extension Study to Evaluate Safety & Tolerability of QR-421a in Subjects With Retinitis PigmentosaWho this might be right forRetinitis PigmentosaUsher Syndrome Type 2 Laboratoires Thea 21
Not applicableStudy completedNCT01325506What this trial is testingEffectiveness of Open and Robotic ProstatectomyWho this might be right forProstate Cancer Beth Israel Deaconess Medical Center 677
Testing effectiveness (Phase 2)Active Not RecruitingNCT06333249What this trial is testingA Study Comparing Two Doses of AGTC-501 in Male Subjects With X-linked Retinitis Pigmentosa Caused by RPGR Mutations (SKYLINE)Who this might be right forX-Linked Retinitis Pigmentosa Beacon Therapeutics 14
Testing effectiveness (Phase 2)Looking for participantsNCT07174726What this trial is testingOpen-label Study to Evaluate the Safety of Laruparetigene Zovaparvovec Administered Bilaterally in Male Participants With X-Linked Retinitis PigmentosaWho this might be right forX-Linked Retinitis Pigmentosa (XLRP) Beacon Therapeutics 10
Not applicableStudy completedNCT04525261What this trial is testingNatural History of Patients With Inherited Retinal Diseases Due to Mutations in RPE65 GeneWho this might be right forLeber Congenital Amaurosis 2Retinitis Pigmentosa 20 University of Campania Luigi Vanvitelli 60
Testing effectiveness (Phase 2)Enrolling By InvitationNCT06275620What this trial is testingA Study Comparing Two Doses of AGTC-501 in Male Participants With X-linked Retinitis Pigmentosa Caused by RPGR Mutations (DAWN)Who this might be right forX-Linked Retinitis Pigmentosa Beacon Therapeutics 24
Testing effectiveness (Phase 2)Study completedNCT01560715What this trial is testingAutologous Bone Marrow-Derived Stem Cells Transplantation For Retinitis PigmentosaWho this might be right forRetinitis Pigmentosa University of Sao Paulo 50